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Here's Why Shares in Agios Pharmaceuticals Popped Today
24 Dec 2025 18:16 GMT
… and Drug Administration (FDA) for AQVESME (mitapivat) for the treatment of … the conference call, the pharmaceutical company's management … (mitapivat is already FDA approved for adults with … with mitapivat in a sickle cell disease trial, and the company is …
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FDA Approves Mitapivat (AQVESME) for Non-Transfusion-Dependent Alpha- and Beta-Thalassemia
24 Dec 2025 17:12 GMT
… US Food and Drug Administration (FDA) has approved mitapivat … under the brand name AQVESME for the treatment … cell survival in sickle cell disease by increasing ATP … randomized, placebo-controlled trial conducted across 70 hospitals …
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AB Science Secures U.S. Patent for Sickle Cell Disease Treatment
23 Dec 2025 07:58 GMT
AB Science has announced that the United States Patent Office has issued a notice of allowance for a patent covering methods of treating sickle cell disease with its flagship molecule, masitinib, based on preclinical results.
The French biopharmaceutical …
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AB Science patent for masitinib in the treatment of sickle cell disease formally granted in the US with a protection until 2040
22 Dec 2025 16:57 GMT
… MASITINIB IN THE TREATMENT OF SICKLE CELL DISEASE FORMALLY GRANTED … for methods of treating sickle cell disease (i.e., … sickle cell disease
Part 2 : Demonstrating in a phase 2 clinical trial … a pharmaceutical company specializing in the research, development …
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Patient dies after taking Pfizer drug for hemophilia
23 Dec 2025 18:26 GMT
… , approved for the treatment of a condition that … disorder drugs. Last year, the company withdrew its sickle cell anemia drug from … announced it was discontinuing development of gene therapy for … receiving US approval. BioMarin Pharmaceutical Inc. is struggling …
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Fight against sickle cell disease: Chhattisgarh screens 1.65 cr persons; 3.35L carriers identified
21 Dec 2025 10:30 GMT
… persons have been screened for sickle cell disease so far in Chhattisgarh … , a key drug used in sickle cell treatment, has increased … of Competence is being developed at All India Institute … towards the elimination of sickle cell disease and will play a …
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Pfizer Reports Patient Death in Long-Term Trial of Hympavzi for Hemophilia A
23 Dec 2025 15:26 GMT
… died, the New York pharma disclosed Monday.
The patient … -term follow up clinical trial featuring Hympavzi, which was … medical conditions and other medications the patient was taking … 2024, Pfizer pulled the sickle cell disease therapy Oxbryta from the market …
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Press Release: Sanofi’s Wayrilz approved in the EU as the first BTK inhibitor to treat immune thrombocytopenia
23 Dec 2025 14:06 GMT
… immune system to develop innovative treatments that make a … the US Food and Drug Administration (FDA) granted Wayrilz ODD … RD), and sickle cell disease (SCD). Wayrilz also received FDA fast track … medicines and vaccines that treat and protect millions of …
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5 most exciting tech innovations of 2025—CRISPR 3, fusion reactions, brain-computer link
24 Dec 2025 17:10 GMT
… and conditions such as sickle-cell disease and inherited blindness. In … tumours that are difficult to treat.
Also read: Top … IPR) in Gandhinagar is developing India’s first fusion electricity … the Food & Drug Administration (FDA) for its ability to …
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YEAR-ENDER - From millennium bug to age of AI: 25 years that reshaped how humanity lives and works
24 Dec 2025 15:05 GMT
… facilitated $1.3 trillion in developer sales.
Advances in touchscreen technology … treatments. In 2023, the first CRISPR-based therapy was approved to treat sickle cell disease … the human body.
In 2023, drugs like Ozempic and Wegovy thrust …