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U.S. Food And Drug Administration Approves CSL's ANDEMBRY® (Garadacimab-Gxii), The Only Prophylactic Hereditary Angioedema (HAE) Treatment Targeting Factor Xiia With Once-Monthly Dosing For All Patients From The Start
17 Jun 2025 01:04 GMT
… Drug Administration (FDA) approved ANDEMBRY® (garadacimab-gxii), the only treatment … antibody discovered and developed entirely by CSL, … is a prescription medication used to prevent attacks … , including those that treat haemophilia and immune deficiencies, …
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Gene therapy offers long-term relief for Haemophilia B: Study
13 Jun 2025 20:03 GMT
… hope for long-term treatment of the rare bleeding … confirming its enduring benefits.
Haemophilia B, an X-linked … trial between 2010 and 2012. Ten adult males with severe haemophilia … was observed shortly after treatment, it was effectively managed …
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This pharma stock surged 10X, crashed 60%, and rose to an all-time high again. Can it sustain the momentum?
09 Jun 2025 13:11 GMT
… medications.
Thereafter, Laurus expanded into the formulation business, where active drugs … supported by a strong drug development pipeline. As of … add 2,500 treatment capacity, to existing … treat genetic disorders such as spinal muscular atrophy, haemophilia …
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The new management concept has bust bureaucracies and brought in greater ownership in teams, says Bayer Pharma India-head
09 Jun 2025 07:57 GMT
… (South Asia), Bayer’s Pharmaceuticals Division – possibly the first … the benefit of these drugs to more patients.
The … first non-hormonal postmenopausal drug (elinzanetant), being applied … — ophthalmology, oncology and haemophilia. There is a pipeline …
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Discovery could improve treatment for people with haemophilia A
28 May 2025 07:16 GMT
… haemophilia A develop resistance to their critical treatment, paving the way for the development … of more effective therapies.
Haemophilia … explain why some people develop resistance to treatment and opens the …
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Pfizer's weekly haemophilia drug backed for NHS use
22 May 2025 11:49 GMT
… few weeks after the drug was approved by the … role of Hympavzi in treating severe haemophilia A, where there … 39;s long-acting FIX drug Altuvoct (efanesoctocog alfa), which … subcutaneous treatment option for severe haemophilia B is a positive development which …
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NICE recommends Pfizer once-weekly treatment for haemophilia B on NHS
21 May 2025 23:23 GMT
… A subcutaneous treatment option for severe haemophilia B is a positive development which … researching and developing new treatment options for people living with haemophilia and are … by NICE for the treatment of haemophilia A, however Pfizer remains …
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ASX biotechs drive paediatric drug advances
21 May 2025 21:08 GMT
… treatments
CSL is a global leader in developing therapies for children with haemophilia … Acadia Pharmaceuticals secured US Food and Drug Administration (FDA) approval for trofinetide to treat … interim analysis of its ACTION3 trial is forecast in around mid …
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MHRA grants UK marketing authorisation for Pfizer’s haemophilia treatment
24 Apr 2025 16:24 GMT
… factor IX inhibitors1.
Discovered and developed by Pfizer scientists, marstacimab targets … eligible patients with a new treatment option. We will continue working … Excellence. Marstacimab for treating severe haemophilia A or severe haemophilia B in people …
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FDA Approved Antihemophilic factor, PEGylated-Aucl For Pediatric Patients With Hemophilia A
19 May 2025 19:32 GMT
… hypersensitivity and loss of drug efficacy due to an … pharmacokinetics, safety, and efficacy of Jivi for prophylaxis and treatment … for this trial was ABR.4
The expanded FDA approval of … previously treated male children with haemophilia a. Updated August 21, …