-
U.S. Department of Health and Human Services Adds Duchenne to Recommended Uniform Screening Panel
16 Dec 2025 17:25 GMT
Parent Project Muscular Dystrophy and Muscular Dystrophy Association Celebrate Monumental Victory for Duchenne Muscular Dystrophy
WASHINGTON, Dec. … Services (HHS) officially added Duchenne muscular dystrophy (Duchenne) to the Recommended Uniform Screening …
-
SMC Approves Givinostat for Duchenne Patients in Scotland
15 Dec 2025 12:13 GMT
… Scotland for the treatment of Duchenne muscular dystrophy (DMD) in patients 6 years … SMC advice was welcomed by Duchenne UK as a “significant breakthrough …
-
Atossa Therapeutics Receives FDA Rare Pediatric Disease Designation for (Z)-Endoxifen for Duchenne Muscular Dystrophy
12 Dec 2025 12:39 GMT
… for the treatment of Duchenne Muscular Dystrophy ("DMD").
RPD … to another company.
About Duchenne Muscular Dystrophy
Duchenne Muscular Dystrophy is a rare, progressive, … -for-z-endoxifen-for-duchenne-muscular-dystrophy-302638744.html
SOURCE Atossa …
-
<![CDATA[Z-Rostudirsen Meets Primary End Point in Phase 1/2 DELIVER Trial for Duchenne Muscular Dystrophy]]>
11 Dec 2025 22:27 GMT
… dystrophin expression among patients with Duchenne muscular dystrophy (DMD) amenable to exon 51 … DMD exon 51.
"The Duchenne community has long awaited therapies …
-
Brothers with muscular dystrophy volunteer IDF
13 Dec 2025 02:44 GMT
… , when he was diagnosed with Duchenne muscular dystrophy, known as DMD.
His parents …
-
RFK Jr. adds fast-moving, debilitating disorders to newborn screening recommendations
16 Dec 2025 21:31 GMT
… . Kennedy, Jr., on Tuesday added Duchenne Muscular Dystrophy and Metachromatic Leukodystrophy disorders to …
-
Health Department Recommends 2 New Conditions for Newborn Screening
16 Dec 2025 18:29 GMT
… F. Kennedy Jr. approved adding Duchenne muscular dystrophy and Metachromatic leukodystrophy, or DMD …
-
Kennedy approves adding two rare disorders to newborn screenings
16 Dec 2025 17:47 GMT
… added two rare genetic disorders, Duchenne Muscular Dystrophy and Metachromatic Leukodystrophy, to the … comment process.
Early detection of Duchenne Muscular Dystrophy (DMD) and Metachromatic Leukodystrophy (MLD …
-
Sarepta Files Three IPRs Against Genzyme’s Patents Related to Gene Therapy Elevidys®
16 Dec 2025 00:57 GMT
… used to treat patients with Duchenne muscular dystrophy (“DMD”) caused by a mutation …
-
ASL Launches iON Integrated Drive Control System
15 Dec 2025 22:02 GMT
… riders with neuromuscular diseases, including Duchenne muscular dystrophy, spinal muscular atrophy, amyotrophic lateral …
About
© 1995-2025