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<![CDATA[Mechanism and Long-Term Outlook of Zeleciment Rosturdirsen in Treating Duchenne Muscular Dystrophy: Doug Kerr, MD, PhD]]>
19 Nov 2025 00:14 GMT
… recovery."
Therapeutic development for Duchenne muscular dystrophy (DMD) has accelerated in recent …
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FDA plans boxed warning, revised indication for Elevidys in children with Duchenne
20 Nov 2025 22:26 GMT
… 4 years and older with Duchenne muscular dystrophy.
In a press release, the … and effective as possible,” the Muscular Dystrophy Association said in a statement …
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FDA Updates Safety Label for ELEVIDYS Gene Therapy for Duchenne Muscular Dystrophy
17 Nov 2025 14:33 GMT
… only approved gene therapy for Duchenne muscular dystrophy (DMD). The revisions, completed in …
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Palm Beach County firefighters unite for marathon to support muscular dystrophy
18 Nov 2025 19:14 GMT
… , HIS WAS DIAGNOSED WITH DUCHENNE MUSCULAR DYSTROPHY. DMD IS A PROGRESSIVE … raise awareness and support for Duchenne Muscular Dystrophy (DMD) through the organization … raise awareness and support for Duchenne Muscular Dystrophy (DMD) through the organization …
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Rapp pushes for additions to newborn screening program
22 Nov 2025 11:33 GMT
… Harrisburg. Her legislation adding Duchenne muscular dystrophy to the state’s Newborn … Committee has approved legislation adding Duchenne muscular dystrophy and Gaucher disease to … Bill 1715 would add Duchenne muscular dystrophy to the program and House …
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<![CDATA[FDA Makes Label Change to Elevidys, ALS Prevalence to Increase by 2040, CNM-Au8 NDA Submitted]]>
22 Nov 2025 12:53 GMT
… ), a marketed gene therapy for Duchenne muscular dystrophy (DMD), to include a new …
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Governor Hochul can lead the nation in gene therapy access for our children
22 Nov 2025 14:02 GMT
… FDA-approved gene therapy for Duchenne’s Muscular Dystrophy, an incurable rare genetic …
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FDA tightens Duchenne gene therapy after deaths of two teens
18 Nov 2025 22:42 GMT
… therapy used to treat Duchenne muscular dystrophy after two teenagers died … infusion designed to slow Duchenne muscular dystrophy, a disease that causes … More information
The Muscular Dystrophy Association has more on Duchenne Muscular Dystrophy.
Copyright © …
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US FDA Restricts Duchenne Gene Therapy Following Fatal Liver Failure Cases in Teens
18 Nov 2025 02:29 GMT
Duchenne muscular dystrophy, or DMD, is a progressive …
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FDA launches investigation into Takeda's Adzynma following reported pediatric death
22 Nov 2025 02:30 GMT
… summer into a pair of Duchenne muscular dystrophy (DMD) patient deaths following treatment …