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'I'm shaking': North Texas mother fights for answers after daughter with Rett syndrome is injured at school, prompting policy review
16 Dec 2025 01:01 GMT
… uses a wheelchair due to Rett syndrome, a neurological disorder.
Although it …
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FDA approves Acadia’s Daybue Stix for Rett syndrome
15 Dec 2025 10:40 GMT
… for oral solution, to treat Rett syndrome.
Rett syndrome is a rare neurodevelopmental disorder … with Daybue oral solution in Rett syndrome patients.
Findings from a bioequivalence … and only approved treatment for Rett syndrome, has provided thousands of …
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Acadia Pharmaceuticals Announces FDA Approval of DAYBUE® STIX for Oral Solution, a New Powder Formulation of Trofinetide for the Treatment of Rett Syndrome
12 Dec 2025 14:26 GMT
… only FDA-approved treatments for Rett syndrome, a rare neurodevelopmental disorder … formulation will remain available. About Rett Syndrome Rett syndrome is a rare, complex, … al. Consensus guidelines on managing Rett syndrome across the lifespan. BMJ …
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Unravel Biosciences Announces Approval by Colombian Health Regulatory Authority to Initiate RVL-001 Clinical Studies for Rett Syndrome and Pitt Hopkins Syndrome
03 Dec 2025 12:50 GMT
… RVL-001 clinical trials for Rett syndrome (“RTT”) and Pitt Hopkins syndrome …
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Down-Regulation of lncRNA CKMT2-AS1 Predicts Poor Prognosis and Promotes Breast Cancer Progression
25 Dec 2025 18:51 GMT
… editing of MECP2 to rescue Rett syndrome neurons. Sci Transl Med. 2023 …
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Profluent and RSRT Partner to Tackle Rett Syndrome with AI-Designed Custom Genomic Medicines
18 Nov 2025 12:58 GMT
… inherited mutations that lead to Rett syndrome, a rare neurodevelopmental disorder. … unmet medical need.”
About Rett Syndrome
Rett syndrome is a rare genetic neurodevelopmental … clock care.
About Rett Syndrome Research Trust
The Rett Syndrome Research Trust is …
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Families fear ‘devastating’ changes to Nebraska program serving people with disabilities, elderly
25 Dec 2025 03:40 GMT
… the hospital. Michaela, who has Rett syndrome, is a beneficiary of the … of Marie Wohlers)
Michaela has Rett syndrome, a rare genetic neurological disorder …
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International Rett Syndrome Foundation Launches Family Listening Sessions to Strengthen Support for Rett Community
28 Oct 2025 10:00 GMT
… families living with Rett syndrome, visit rettsyndrome.org.
About Rett Syndrome
Rett syndrome is a rare … leading to identifying Rett syndrome's cause, demonstrating Rett syndrome is reversible in …
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Raymond James Initiates Strong Buy on Taysha (TSHA) Amid Rett Syndrome Trial Momentum
27 Oct 2025 19:15 GMT
… Buy on Taysha (TSHA) Amid Rett Syndrome Trial Momentum Pressmaster/Shutterstock … ;2 REVEAL trial results for Rett syndrome and positive FDA feedback as … focus on a genetically defined Rett syndrome population offers a clear therapeutic …
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Murphy Elementary presents Purple Out to support student with Rett Syndrome
22 Oct 2025 05:44 GMT
… raised funds for the International Rett Syndrome Foundation by purchasing specially … event.
According to the International Rett Syndrome Foundation, the disease is … clinically diagnosed individuals. While Rett Syndrome most commonly occurs in females …