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Murphy Elementary presents Purple Out to support student with Rett Syndrome
22 Oct 2025 05:44 GMT
… raised funds for the International Rett Syndrome Foundation by purchasing specially … event.
According to the International Rett Syndrome Foundation, the disease is … clinically diagnosed individuals. While Rett Syndrome most commonly occurs in females …
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Kezar seeks strategic alternatives after FDA setback; Taysha, Astellas' Rett syndrome agreement expires
17 Oct 2025 16:06 GMT
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Taysha Gene Therapies Regains Full Rights to Lead TSHA-102 Program in Clinical Evaluation for the Treatment of Rett Syndrome
16 Oct 2025 20:01 GMT
… the developmental plateau population of Rett syndrome. The primary endpoint will … products Regulatory Agency. About Rett Syndrome
Rett syndrome is a rare neurodevelopmental disorder … and shortened life expectancy. Rett syndrome progression is divided into four …
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Experts argue medical marijuana bill lacks regulations but advocates say it would be a relief
23 Oct 2025 17:19 GMT
… from a neurological disorder called Rett syndrome, said her friends who have …
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<![CDATA[Trofinetide Leads to Real-World Improvements in Rett Syndrome Symptoms, LOTUS Study Finds]]>
13 Oct 2025 23:25 GMT
… prospective study of individuals with Rett syndrome (RTT) on trofinetide (Daybue; … points: change from baseline in Rett Syndrome Behaviour Questionnaire (RSBQ) total score … (trofinetide) for the Treatment of Rett Syndrome in Adult and Pediatric Patients …
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Neurogene Announces Positive Regulatory Update for NGN-401 Gene Therapy in Rett Syndrome with Plans to Initiate Dosing in Embolden™ Registrational Trial in Q4 2025
09 Oct 2025 13:57 GMT
… reaching key brain regions underlying Rett syndrome
As previously reported, the … one-time gene therapy for Rett syndrome
Title: Hemophagocytic lymphohistiocytosis (HLH)… advancement in gene therapy for Rett syndrome, specifically because the disorder …
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Taysha Gene Therapies Presents New Supplemental Data Analysis from Part A of the REVEAL Phase 1/2 Trials for TSHA-102 in Rett Syndrome at the 54th CNS Annual Meeting
09 Oct 2025 12:00 GMT
… (R-MBA) evaluating specific Rett syndrome disease characteristics (N=10 patients … products Regulatory Agency. About Rett Syndrome
Rett syndrome is a rare neurodevelopmental disorder … and shortened life expectancy. Rett syndrome progression is divided into four …
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SJCA Volleyball Purple Out supports people with Rett Syndrome
09 Oct 2025 05:02 GMT
… financial support for families with Rett syndrome.
Thea Day, a … raise awareness for Rett Syndrome — not only for Rett Syndrome itself, but … to raise awareness for Rett syndrome and help families with … the ribbon color for Rett syndrome, which is a genetic …
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Neurotech scores US FDA rare disease win for NTI164 in Rett syndrome
08 Oct 2025 02:58 GMT
… s NTI164 for treatment of Rett syndrome
Designation helps facilitate innovative …
Rare paediatric disease affecting girls
Rett syndrome is a rare genetic neurological … underscores its therapeutic potential for Rett syndrome.
“Combined with the existing …
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Biomed Industries, Inc. to Present Promising NA-921 Phase 2/3 Results for Rett Syndrome Treatment at EAPS 2025
06 Oct 2025 10:00 GMT
… to 20 years diagnosed with Rett syndrome (ClinicalTrials.gov Identifier: NCT06849973). … safety.
AN UNMET NEED IN RETT SYNDROME
Rett syndrome is a rare and severe … currently no curative treatments for Rett syndrome. Management strategies focus on …
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