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Apple snail eye regeneration offers new insights into human sight restoration
06 Aug 2025 13:12 GMT
… better understand and find treatments for eye conditions … identify solutions for treating conditions like retinal degeneration or physical … at where regeneration and development diverge and are … genetic mechanisms behind mollusk development."
For each …
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Ocugen doses first patient in phase 2/3 GARDian3 pivotal confirmatory trial of OCU410ST for Stargardt disease
22 Jul 2025 11:38 GMT
… trial for OCU410ST - a modifier gene therapy candidate being developed … for approvals.”
"Treating the first patient with … vision with no approved treatment options. The encouraging … eye disorder that causes retinal degeneration and vision loss. Stargardt …
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Ocugen doses first subject in trial of modifier gene therapy candidate
21 Jul 2025 12:08 GMT
… II/III GARDian3 trial of modifier gene therapy candidate … that will not receive the treatment.
GARDian3’s primary goal … leading to vision loss and retinal degeneration.
In March 2025, Ocugen … Phase I trial of OCU200, a fusion protein for treating diabetic …
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Gene Therapy for Inherited Macular Degeneration Begins Pivotal Trial
18 Jul 2025 20:48 GMT
… trial. OCU410ST, which is being developed by Ocugen, is a possible treatment … eye disorder that causes retinal degeneration and vision loss in … executives from Ocugen. The FDA has granted a Rare Pediatric … phase 1/2 trial to treat dry age-related macular …
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Retinal Degeneration Fund to Support Opus Genetics’ OPGx-MERTK Gene Therapy Program
30 Jun 2025 16:37 GMT
… funding agreement with the Retinal Degeneration Fund (RD Fund), … is currently in preclinical development, targeting a rod- … for which no approved treatments currently exist.
Strategic Partnership … asset towards Investigational New Drug enabling studies. We …
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Ocugen, Inc. Announces First Patient Dosed in Phase 2/3 GARDian3 Pivotal Confirmatory Trial for OCU410ST—Novel Modifier Gene Therapy Candidate for Stargardt Disease
18 Jul 2025 11:02 GMT
… trial for OCU410ST (AAV5-hRORA)—a modifier gene therapy candidate being developed … for approvals.” "Treating the first patient with … vision with no approved treatment options. The encouraging … eye disorder that causes retinal degeneration and vision loss. …
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Retinal Degeneration Fund providing funding to Opus Genetics to support OPGx-MERTK program
28 Jun 2025 14:50 GMT
… an agreement with the Retinal Degeneration Fund (RD Fund), … gene therapies are developed to treat patients with retinitis pigmentosa … asset towards Investigational New Drug enabling studies. We are … virus vector for the treatment of MERTK-associated inherited …
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FDA grants fast track designation to Sanofi’s SAR446597
17 Jul 2025 12:24 GMT
… US Food and Drug Administration (FDA) has granted fast … hasten the development and review of new drugs that … delivery of significant new medications to patients, encompassing … treating patients with neovascular wet AMD.
AMD is a progressive retinal degeneration …
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Nanoscope Therapeutics Puts Rolling BLA for Retinitis Pigmentosa Gene Therapy MCO-010 in Front of FDA
16 Jul 2025 06:46 GMT
… phase 2b RESTORE clinical trial (NCT04945772), which met … step toward developing a universal treatment for retinal … FDA for MCO-010, the first gene-agnostic therapy to treat … vision in patients with severe retinal degeneration, Molecular Therapy (2025), …
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First Patient Dosed in Phase 1 Trial of PulseSight Therapeutics’ PST-611 for Dry AMD/GA
08 Jul 2025 20:52 GMT
… vectorized therapy designed to treat dry AMD/GA … retinal degeneration.
Details of the Phase 1 Study
The PST-611-CT1 trial … trials:
“Having pioneered the development of the electro-transfection … to become a major treatment option for these patients.” …