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Bangladeshi generic version slashes rare disease drug’s price by 96%
24 Oct 2025 12:49 GMT
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Popular actress dead at 23 after battle with rare disease
24 Oct 2025 09:17 GMT
Isabelle Tate, a popular young actress who was just really getting going in the business, has died.
She was 23.
Tate recently appeared in the pilot episode of “9-1-1” Nashville.”
“We are deeply saddened and completely heartbroken to share that Isabelle …
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<![CDATA[Roundup: Pharma Industry Raises Funding Aimed at Advancing the Development and Testing of Rare Disease Treatments ]]>
24 Oct 2025 02:28 GMT
… clinical trials and testing for rare disease treatments. Companies involved in the …
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BGPD hosts ‘day full of smiles’ for boy with rare disease
23 Oct 2025 20:25 GMT
… hosted a toddler with a rare disease for “a day full of … and spinal surgery for a rare disease, stopped by the Bowling Green …
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Dani, the little boy from Malaga with a rare disease who is undergoing pioneering therapy in Spain
23 Oct 2025 19:06 GMT
… for children with cancer or rare diseases, which took Dani to the … in the fight against his rare disease
Dani's referral doctor …
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Fundraiser organized for girl with rare disease in need of wheelchair accessible van
23 Oct 2025 16:11 GMT
LONG BEACH, Miss. (WXXV) — Brighton is a 3-year-old girl from Long Beach who has a rare, mitochondrial disorder and is in need of a wheelchair accessible van.
Brighton was born with Leigh Syndrome, a rare, progressive, and terminal mitochondrial disease …
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Maggie's Haunted Classic hockey tournament raises funds for rare disease
23 Oct 2025 04:46 GMT
KENNEWICK, Wash. – The 2nd Annual Maggie's Haunted Classic Hockey Tournament is set to take place this weekend at the Toyota Arena. The event focuses on raising funds for research into the rare FOXP1 disease.
Last year's tournament featured 12 …
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Kentucky police department hosts ‘day full of smiles’ for boy with rare disease
22 Oct 2025 23:51 GMT
… hosted a toddler with a rare disease for “a day full of … and spinal surgery for a rare disease, stopped by the Bowling Green …
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Sanofi drug acquired in buyout succeeds in rare disease trial
22 Oct 2025 18:33 GMT
French pharmaceutical company Sanofi said Wednesday an experimental drug it acquired in a buyout last year succeeded in a mid-stage trial against a rare liver and lung disease.
According to Sanofi, the drug, known efdoralprin alfa, met all of its main and …
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Sanofi reveals Phase 2 rare disease win from Inhibrx buyout
22 Oct 2025 16:36 GMT