… an aspiration. Though all rare disease patients encounter substantial barriers to … scans, can help doctors recognize rare diseases more quickly and accurately, … outcomes for rare disease patients. Because in the fight for rare disease equity, technology …

… unity, perseverance, and progress for rare diseases and rare families around the …

… health and lives.” Esteve deepens rare disease focus with endocrinology expansion Furthermore … on the rare and ultra-rare disease space, specifically pertaining to endocrinology …

… funding treatment for children battling rare diseases through sporting events. The partnership …

… , societal and scientific imperative. In rare diseases, where patients often face delayed … fraction of all patients. In rare diseases, where diagnosis can take years … , resources many people living with rare diseases don’t have. Carers, shift …

… , which generated positive results in rare disease familial chylomicronaemia syndrome (FCS) last …

… doing enough to support rare disease innovation? Enrico Piccinini: Rare disease R&D … demonstrating safety and efficacy under rare disease conditions. EV: Are new … Piccinini: Diagnosis can take years. Rare diseases often affect multiple organs, so …

… . VIDEO: Rare disease paralyzes 3-year-old, parents urge vigilance Rare disease paralyzes 3 …

Sam Ramsay was drafted by AFL club Carlton    Teammates making sacrifice to help 24–year–old  By SHAYNE BUGDEN Published: 23:12 EDT, 2 August 2025 | Updated: 23:12 EDT, 2 August 2025 Footy star Sam Ramsay has learned that the 'back pain' that has …

… to raise awareness about a rare disease. It's a journey …