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US FDA approves PTC Therapeutics’ Sephience to treat children and adults living with phenylketonuria
30 Jul 2025 09:29 GMT
… children and adults living with phenylketonuria (PKU). The approval includes broad … adult and paediatric patients with phenylketonuria (PKU). Sephience is a natural … a phenylalanine (Phe)-restricted diet.
Phenylketonuria (PKU) is a rare, inherited …
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PTC’s Sephience wins FDA nod for phenylketonuria
30 Jul 2025 01:30 GMT
… . will be launching its oral phenylketonuria therapy, Sephience (sepiapterin) in both …
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FDA approves sepiapterin to treat phenylketonuria in adult, pediatric patients
29 Jul 2025 01:36 GMT
… adult and pediatric patients with phenylketonuria (PKU), including all age groups … Children and Adults Living with Phenylketonuria (PKU). PTC Therapeutics. Press release …
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Phenylketonuria Pipeline Outlook Report 2025: Key 20+ Companies And Breakthrough Therapies Shaping The Future Landscape
29 Jul 2025 00:25 GMT
… .....
Inactive Products
Phenylketonuria Key Companies
Phenylketonuria Key Products
Phenylketonuria- Unmet Needs
Phenylketonuria- Market Drivers …
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FDA Approves Sepiapterin for Adults, Children Living With Phenylketonuria
28 Jul 2025 23:05 GMT
… adults and children living with phenylketonuria (PKU), a rare, inherited … Children and Adults Living with Phenylketonuria (PKU). News Release. Released April … of PTC923 in Participants With Phenylketonuria. National Library of Medicine. ClinicalTrials …
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PTC Therapeutics Announces FDA Approval of Sephience™ (sepiapterin) for the Treatment of Children and Adults Living with Phenylketonuria (PKU)
28 Jul 2025 21:19 GMT
… children and adults living with phenylketonuria (PKU). The approval includes broad … adult and pediatric patients with phenylketonuria (PKU). Sephience is a … see Full Prescribing Information.
About Phenylketonuria
Phenylketonuria (PKU) is a rare, inherited …
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Rare Disease Show - Episode 25: Understanding Phenylketonuria ft Dr Roshan Daniel, KIMSHEALTH
15 Jul 2025 21:59 GMT
… ;s show we will cover Phenylketonuria.
Phenylketonuria (PKU) is a rare inherited … is the genetic basis of Phenylketonuria, and how is it inherited …
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Germany will be first launch for PTC's phenylketonuria drug
25 Jun 2025 15:28 GMT
… ; treatment for the rare disease phenylketonuria (PKU), Sephience, setting up a …
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PTC Therapeutics’ Sephience gets European marketing authorization to treat children and adults living with phenylketonuria
24 Jun 2025 08:38 GMT
… children and adults living with phenylketonuria (PKU). The authorization includes a … adult and pediatric patients with phenylketonuria (PKU). Sephience is a natural … drug in the United States.
Phenylketonuria (PKU) is a rare, inherited …
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Sephience™ (sepiapterin) Granted Marketing Authorization by the European Commission for the Treatment of Children and Adults Living with Phenylketonuria (PKU)
23 Jun 2025 12:16 GMT
… children and adults living with phenylketonuria (PKU). The authorization includes a … adult and pediatric patients with phenylketonuria (PKU). Sephience is a natural … in the United States.
About Phenylketonuria
Phenylketonuria (PKU) is a rare, inherited …