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Family enlists Harvard scientists in fight against rare neurological disorder
26 Sep 2025 21:37 GMT
… mice that received the treatment experienced fewer and less … have the potential to treat genetic neurological conditions beyond … editing to rescue a neurological disease. We looked at the … patients, and scientists that had developed around the disorder. Soon, …
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AbbVie Submits NDA for Parkinson’s Disease Drug, Tavapadon
26 Sep 2025 18:49 GMT
… vice president, research and development and chief scientific officer, … s is a progressive neurological disorder caused by the death … no cure, there are treatments that can lessen symptoms, … drugs that reduce tremors.
Most FDA-approved Parkinson’s medications …
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Diabetes drug Liraglutide cuts migraine days in half
26 Sep 2025 17:21 GMT
… showing promise as a treatment beyond weight loss. ( … and weight-control medication liraglutide could sharply … drug repurposing. That’s where a drug developed for one disease ends up treating … a diabetes drug might now cure a common neurological disorder. It …
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Serum Metabolic and Gut Microbiome Differences in Age-Associated Fragile X Syndrome (FXS) Pediatric Patients May Benefit Clinical Therapy Development
26 Sep 2025 10:58 GMT
… microbiota in human neurological disorders has gained increasing … in the treatment of neurological disorders.13–15 … unreported in normal development, highlights disease-specific … Dehydroepiandrosterone (DHEA): pharmacological effects and potential therapeutic …
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Arialys Therapeutics Receives FDA Rare Pediatric Disease Designation for ART5803 to Treat Anti-NMDA Receptor Encephalitis
26 Sep 2025 06:18 GMT
… .S. Food and Drug Administration (FDA) has granted Rare … the development of new drugs and biologics for the treatment … structures and pharmacological assessments to develop ART5803 as … managed, and often misdiagnosed neurological disease. ANRE is caused by …
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Researchers develop tool to predict how patients will respond to common multiple sclerosis drug
26 Sep 2025 02:47 GMT
… French institutions, have developed a tool that can … most commonly used drugs for treating multiple sclerosis.
Despite … poor outcomes with natalizumab treatment are associated with … , inflammatory, and degenerative neurological disease that affects the central …
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Health Canada Says Tylenol Safe During Pregnancy, Rebuffs US FDA Autism Concerns
26 Sep 2025 02:23 GMT
… can cause autism or other neurological disorders in children.
The agency made … after the U.S. Federal Drug Administration (FDA) said there may be …
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Hope for sufferers of devastating brain disease as new treatment has 75% success rate
26 Sep 2025 00:54 GMT
… gene therapies for the treatment of neurological disorders,” Dr. Walid Abi- … have a 50% chance of developing Huntington’s.
The genetic … .com
In the uniQure trial, 12 of 29 patients … symptoms can be managed through medications, physical, speech and occupational …
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SciSparc’s Stock Explodes on Quantum Leap into Drug Discovery Revolution
26 Sep 2025 00:49 GMT
… SciSparc, this scrappy Israeli pharma player out of Tel Aviv … new drugs. Get it right, and you could unlock treatments for … could turbocharge drug hunts for tough nuts like neurological disorders and rare … but slow—years of trial and error, billions flushed …
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Pharmaceutical Executive Daily: September 25, 2025
25 Sep 2025 23:27 GMT
… Hengrui, Harmony Biosciences’ trial setback for Zygel, and … Pharma for trastuzumab rezetecan, a next-generation antibody-drug … addressing unmet needs in neurological disorders but acknowledged the … reassessment of Zygel’s development path. Investors responded …