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Scientists apply genome editing to treat muscular dystrophy
03 Feb 2026 22:29 GMT
… more effective treatment for a certain type of muscular dystrophy.
The … Kyoto University and Takeda Pharmaceutical Co.
The ultimate goal … damaged.
Traditional treatment typically relied on medication for removing part … delivery via a mouse trial, as muscle stem …
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Senator Collins secures key health care and education funds for Maine in federal budget
04 Feb 2026 17:04 GMT
… of Medicare coverage policies regarding FDA-approved therapies.
Funding is maintained … include $9 million for CDC Muscular Dystrophy activities; $27 million for CDC … HEAL Initiative. Data shows that drug overdose deaths continue a downward …
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Patent losses hit Novartis hard, but CEO has a plan
04 Feb 2026 11:01 GMT
… company is expecting seven pivotal trial readouts this year and 28 … involving new drugs like immunology therapy ianalumab, Ionis-partnered cardiovascular drug pelacarsen … zotadirsen (del-zota) for Duchenne muscular dystrophy (DMD).
Novartis needs that pipeline …
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Entrada Therapeutics to Present at Upcoming Investor Conferences
04 Feb 2026 12:00 GMT
BOSTON, Feb. 04, 2026 (GLOBE NEWSWIRE) -- Entrada Therapeutics, Inc. (Nasdaq: TRDA) today announced the Company will participate in two upcoming investor conferences. Guggenheim Emerging Outlook: Biotech Summit 2026
Dipal Doshi, Chief Executive Officer, …
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New $100M CIRM Initiative Centers Platform Approaches for Rare Genetic Diseases
03 Feb 2026 14:42 GMT
… , including LAD-1, forms of muscular dystrophy, Danon syndrome, Machado-Joseph disease … the U.S. Food and Drug Administration.
CIRM’s RAPID program … have already engaged with the FDA and received pre-IND feedback …
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Bipartisan Congressional Action Advances Critical Programs for Rare Neuromuscular Disease Research and Care
03 Feb 2026 20:03 GMT
… diseases, including Duchenne muscular dystrophy, spinal muscular atrophy, … more than 30 FDA-approved treatments in just the … which there is no treatment. She has spent … @mdausa.org About Muscular Dystrophy Association
Muscular Dystrophy Association (MDA) has …
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Shriners Children’s Philadelphia earns top national recognition for pediatric musculoskeletal surgery
04 Feb 2026 00:52 GMT
… during ACS verification. The hospital treats various musculoskeletal conditions such as … differences, gait abnormalities, cerebral palsy, muscular dystrophy, clubfoot and others.
She noted … children can expect when receiving treatment there.
As one out of …
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RESTEM Announces First Patient Dosed in the Phase 2/3 IIMPACT Study of Restem-L in Idiopathic Inflammatory Myopathy
03 Feb 2026 18:06 GMT
… our Phase 1 trial, which demonstrated … Food and Drug Administration (FDA) for the treatment of … study in Facioscapulohumeral Muscular Dystrophy (FSHD). About Idiopathic … treat. Currently, the treatments for these disorders are various immunosuppressive drugs …
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[Latest] Global Adeno Associated Virus Vector Manufacturing Market Size/Share Worth USD 9.87 Billion by 2035 at a 13.4% CAGR: Custom Market Insights (Analysis, Outlook, Leaders, Report, Trends, Forecast, Growth Rate, Value, SWOT Analysis)
03 Feb 2026 18:00 GMT
… conditions as Duchenne muscular dystrophy, hemophilia, spinal muscular … to late-stage drug trials and commercialization, … good regulatory systems (FDA), attractive reimbursement channels, … and Insights By Product (Pharmaceuticals, Parasiticides, Anti-infectives …
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Prevention of HIV, Protection Against Influenza Without Vaccines. Medical Breakthroughs of 2025
03 Feb 2026 14:22 GMT
… diseases they will help treat, citing material from … new drugs were evenly distributed between large pharmaceutical companies and … treatment of ovarian cancer was developed, and a drug … also noted that Duchenne muscular dystrophy has long remained a …