-
Hyderabad teen with muscular dystrophy shines at international chess championship
06 Aug 2025 11:51 GMT
… 18-year-old battling Duchenne Muscular Dystrophy, competed in the World IPCA … has been bravely battling Duchenne Muscular Dystrophy (DMD), a rare and severe …
-
Meath couple take on walking challenge from Letterkenny to the green fields of Enfield in aid of Muscular Dystrophy Ireland
06 Aug 2025 05:36 GMT
Parents Paddy and Claire Hickey are planning to walk over 200km from Letterkenny, Co. Donegal to their home town of Enfield, Co. Meath to raise awareness about the neuromuscular condition, Bethlem myopathy.
-
Dyne Therapeutics Announces FDA Breakthrough Therapy Designation for DYNE-251 in Duchenne Muscular Dystrophy (DMD)
04 Aug 2025 11:30 GMT
… treatment of patients with Duchenne muscular dystrophy (DMD), amenable to … 251 in individuals with Duchenne muscular dystrophy (DMD) who have … and Duchenne muscular dystrophy (DMD), and preclinical programs for facioscapulohumeral muscular dystrophy (FSHD) …
-
Research Tip Sheet: Heart Attack, Muscular Dystrophy, Neuroprosthetics
02 Aug 2025 02:54 GMT
… Therapy Prevents Damage From Duchenne Muscular Dystrophy
A cell therapy preserves muscle … Institute at Cedars-Sinai.
Duchenne muscular dystrophy is a rare, inherited … the natural progression of Duchenne muscular dystrophy.
Other Cedars-Sinai authors include …
-
Outrage of the Month: Patient Deaths From a Duchenne Muscular Dystrophy Gene Therapy
01 Aug 2025 19:02 GMT
… approved gene therapy for Duchenne muscular dystrophy linked to three patient deaths … therapy for both types of muscular dystrophy.
Subsequently, the FDA announced that … therapies are needed for Duchenne muscular dystrophy, a rare but devastating genetic …
-
Keros Therapeutics Reports Second Quarter 2025 Financial Results
06 Aug 2025 20:01 GMT
… trial in patients with Duchenne muscular dystrophy in the first quarter of … an initial focus on Duchenne muscular dystrophy. Keros’ most advanced product candidate …
-
Sarepta’s Future in Gene Therapy Remains Clouded, But Data From Partner Hansa Is a Bright Spot
06 Aug 2025 20:40 GMT
… injury from its commercialized Duchenne muscular dystrophy gene therapy. But Sarepta partner … a type of limb-girdle muscular dystrophy.
The FDA initially asked Sarepta … both Duchenne and limb girdle muscular dystrophies. Beyond the $10 million …
-
Keros to Exclusively Prioritize the Clinical Advancement of KER-065
06 Aug 2025 20:15 GMT
… for individuals living with Duchenne muscular dystrophy (“DMD”),” said Jasbir S. Seehra … an initial focus on Duchenne muscular dystrophy. Keros’ most advanced product candidate …
-
Catalyst Pharmaceuticals Reports Record Second Quarter and First Half 2025 Financial Results; Provides Business Update
06 Aug 2025 20:13 GMT
… potential benefits over other Duchenne muscular dystrophy (DMD) treatments, such as in …
-
The Health Wrap: updates on Trump et al, spotlight on liver diseases, good news on malaria – and beauty in all seasons
06 Aug 2025 17:48 GMT
… controversial gene therapy for Duchenne muscular dystrophy that has been linked to …