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3 BLAs in 3 Years: Ocugen Sees Potential in Eye Disease Gene Therapies
06 Aug 2025 06:52 GMT
… disease such as RP or Leber congenital amaurosis (LCA), and enough viable retinal …
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Gene therapy for Leber congenital amaurosis has positive phase 1/2 results at 12 months
26 Jun 2025 21:06 GMT
… -LCA5, a gene therapy for Leber congenital amaurosis.
She presented 12-month results … -LCA5 for the treatment of Leber congenital amaurosis, as Healio previously reported.
Sources …
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AAV for the Hereditary Retinal Diseases Clinical Trial Pipeline Analysis Demonstrates 70+ Key Companies at the Horizon Expected to Transform the Treatment Paradigm, Assesses DelveInsight
05 Aug 2025 17:00 GMT
… defects lead to disorders like Leber congenital amaurosis (LCA), retinitis pigmentosa, … These disorders, such as Leber congenital amaurosis (LCA), retinitis pigmentosa, and … treat patients diagnosed with Leber congenital amaurosis (LCA) resulting from …
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Opus Genetics to Participate in the H.C. Wainwright 5th Annual Ophthalmology Virtual Conference
05 Aug 2025 12:00 GMT
… targeting inherited retinal diseases including Leber congenital amaurosis (LCA), bestrophinopathy, and retinitis pigmentosa …
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Global Leber Congenital Amaurosis Market 2025-2034: Growth, Share, Segments & Emerging Trends Analysis
13 May 2025 17:14 GMT
… the Growth of the Leber Congenital Amaurosis Market?
The leber congenital amaurosis market is expected to … ;leber-congenital-amaurosis-global-market-report
How Is the Leber Congenital Amaurosis Market Segmented?
The leber congenital amaurosis …
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FDA grants RMAT designation to gene therapy for Leber congenital amaurosis
08 May 2025 01:12 GMT
… -LCA5 for the treatment of Leber congenital amaurosis due to genetic variations in …
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MeiraGTx Announces The Lancet Publication of Data Demonstrating the Efficacy of rAAV8.hRKp.AIPL1 for the Treatment of Leber Congenital Amaurosis 4 (LCA4) Retinal Dystrophy
21 Feb 2025 11:30 GMT
… the most severe forms of Leber congenital amaurosis 4 (LCA4) owing to genetic …
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MeiraGTx Receives Rare Pediatric Disease Designation from FDA for AAV8-RK-RetGC for the Treatment of Patients with Leber Congenital Amaurosis due to GUCY2D Mutations
22 Jan 2025 13:30 GMT
… the treatment of patients with Leber congenital amaurosis due to GUCY2D mutations (LCA1 … of cases causing autosomal recessive Leber congenital amaurosis type 1 (LCA1) whilst … the most severe forms of Leber congenital amaurosis (LCA) owing to genetic …
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Opus Genetics partners with Global RDH12 Alliance
31 Jul 2025 23:36 GMT
… for the potential treatment of Leber congenital amaurosis (RDG12-LCA).1 To deliver …
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Opus Genetics and Global RDH12 Alliance announce partnership
30 Jul 2025 19:16 GMT
… for the potential treatment of Leber congenital amaurosis (RDG12-LCA).1 To deliver …
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