… trial for a Regenxbio gene therapy developed a brain tumor … implications for another Regenxbio gene therapy expected to receive a … participant who received the gene therapy four years ago. … 121, Regenexbio’s experimental gene therapy for Hunter syndrome, …

… -associated virus vector-based gene therapy TSHA-102 for the … intrathecal dose of the gene therapy at 1x1015 total vector … BLA submission for the gene therapy aimed at an indication … progress across TSHA-102 pivotal gene therapy program in Rett syndrome. …

… ), making it the first retinal gene therapy to do so in Japan … regulatory strategies in optogenetic retinal gene therapy for patients living with inherited …

… the efficacy of an Strc gene therapy in a mouse model of … and throat Neurology/psychiatric Gene therapy

… and capsid titers in AAV gene therapy manufacturing. “The NanoMosaic technology … , and scalability across AAV gene therapy manufacturing, according to Philippe … control measures that meaningfully advance gene therapy manufacturing,” he continues. NanoMosaic …

… applications. Growth in mRNA vaccine gene therapy development, expanding pharmaceutical and biotechnology … , particularly for oligonucleotide synthesis in gene therapy and diagnostic development. Government investment …

… first local and national gene therapy research product. The project … significant progress in gene therapy that will improve … of producing an investigational gene therapy for a genetic … instance, we perform intracranial gene therapy. Our teams undergo very …

… for UX111 (rebisufligene etisparvovec) AAV9 gene therapy as a treatment for patients … a novel in vivo AAV9 gene therapy in Phase 1/2 …

… associated virus (AAV) vector-based gene therapy intended to treat Stargardt disease … the potential of this modifier gene therapy platform approach to transform treatment … approval pathway for OCU410ST—modifier gene therapy for Stargardt disease. News release …