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CRISPR Brings Genes Closer Together in New Approach to Gene Therapy
20 Jun 2025 09:36 GMT
… gene’. The broader field of gene therapy could thus benefit from delete … to the currently available gene therapy. While the existing gene therapy was approved for …
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Rznomics' gene therapy selected for Korea's national drug development project
20 Jun 2025 05:08 GMT
… Friday that its anticancer gene therapy RZ-001 had been selected … of RZ-001, an anticancer gene therapy drug for glioblastoma, for … 001 is a next-generation gene therapy that targets and cleaves … a first-in-class anticancer gene therapy based on our long- …
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Japan Gene Therapy Market Growth: $148.06M in 2024 to $904.94M by 2033 | CAGR 20.3%
20 Jun 2025 04:48 GMT
… sample/japan-gene-therapy-market
Regional Outlook
Gene therapy is gaining ground … a leader in the APAC gene therapy market.
Company Landscape
Alnylam … DataM intelligence
Gene Therapy Market Size 2025-2033
Cancer Gene Therapy Market Size …
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Sickle Cell Disease Pediatric Gene Therapy Program Offers Children Hope for a Cure
19 Jun 2025 19:42 GMT
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FDA’s gene therapy turmoil, and an alternative model for funding research
19 Jun 2025 19:15 GMT
… oust one of its top gene therapy regulators? Is the agency growing … died after taking Sarepta Therapeutics’ gene therapy, raising renewed questions about the … the forced dismissal of top gene therapy regulator Nicole Verdun, as well …
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STAT+: What’s next for Sarepta Therapeutics with gene therapy under fire?
19 Jun 2025 19:15 GMT
… failure caused by Sarepta Therapeutics’ gene therapy Elevidys. On Monday, my colleague …
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Updates in Gene Therapy, Biomarkers, and AI Advancements for ALS Care Management
19 Jun 2025 18:27 GMT
… ; Biogen), the first FDA-approved gene therapy targeting SOD1 mutations, as a … tofersen, which is the first gene therapy for ALS. This is only …
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Seeing Beyond Sight: New Frontiers in AMD Treatment-Gene Therapy and Biosimilars Take Center Stage | CI Intelligence
19 Jun 2025 17:53 GMT
… competition, reimbursement reforms, and gene therapy innovations are key drivers shaping … (4D Molecular Therapeutics): Intravitreal gene therapy targeting VEGF-A and VEGF … expanding patient population.
- Gene therapy and biosimilars are expected to …
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FDA's top cell and gene therapy leaders leave agency
19 Jun 2025 17:14 GMT
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Second Death Reported After Elevidys Gene Therapy; FDA and Sarepta Investigating
19 Jun 2025 15:19 GMT
… Elevidys, the only FDA-approved gene
therapy for Duchenne muscular dystrophy (DMD … patients during our review of gene therapy products,” the agency said in … “overrode 3 reviewers to approve gene
therapy that kills more boys than …