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Gene Therapy Momentum Builds Among Hematologists in Sickle Cell Disease Management Despite Ongoing Access Barriers, According to Spherix Global Insights
01 May 2025 15:42 GMT
… patients, “long-term, gene therapy is the solution”. Just … referred a patient for gene therapy, or in some cases … least a discussion about gene therapy, whether now or in … new therapies – including options beyond gene therapy – are in development, promising …
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FDA approves Abeona’s epidermolysis bullosa gene therapy Zevaskyn
01 May 2025 11:21 GMT
… the first autologous cell-based gene therapy approved in the US to …
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Siren, a gene therapy startup, tests unconventional alternative to venture funding
01 May 2025 10:46 GMT
… , a San Francisco-based gene therapy startup, has already done … that blends elements of gene therapy and cancer immunotherapy. It … doesn’t mention the gene therapy field’s recent headwinds, … potential of AAV immuno-gene therapy for patients,” Fischer wrote …
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More Innovative Cell and Gene Therapy Payment Strategies Needed, Expert Says | Asembia's AXS25 Summit
01 May 2025 04:24 GMT
… challenges in the cell and gene therapy space, more innovative payment models … that in the cell and gene therapy space, there have been several …
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Gene therapy shows promising results for kids with severe immune disorder
01 May 2025 03:36 GMT
… years after receiving an investigational gene therapy, nine children diagnosed with severe … childhood experiences.
The investigational lentiviral gene therapy, currently unapproved for clinical use …
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Boy with ‘death sentence’ disease living a normal life after breakthrough gene therapy
01 May 2025 01:22 GMT
… enrolled him in a groundbreaking gene therapy trial at Great Ormond Street … the operation before the gene therapy.
After the successful gene therapy, which has been … showed “normal wound healing” after gene therapy.
The author, including experts from …
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FDA Approves First Cell-Based Gene Therapy For Rare Skin Disorder
01 May 2025 01:19 GMT
… (FDA) has approved Zevaskyn, a gene therapy for a rare skin disorder … is the first cell-based gene therapy to receive approval for the … Drug Administration approved Vyjuvek, a gene therapy from Krystal Biotech, in 2023 …
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Around the Helix: Cell and Gene Therapy Company Updates – April 30, 2025
01 May 2025 00:18 GMT
The cell and gene therapy sectors are growing …
Have a cell and gene therapy news update you’d … clinical development of its optogenetic gene therapy, RTx-015. “Retinitis … marketed as Adstiladrin), a gene therapy currently approved for the treatment …
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Gene Therapy Restores Immune Function and Extends Lives of Children with Rare Immune Disorder
30 Apr 2025 23:23 GMT
… Ani Vahradyan
Newswise — An investigational gene therapy has successfully restored immune function … results underscore the potential of gene therapy to provide “durable, life … license for this investigational lentiviral gene therapy is currently held by …
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Global Leaders Talk Stem Cell Research And Gene Therapy
30 Apr 2025 23:16 GMT
NASSAU, BAHAMAS – HEALinc, which stands for health, self-efficacy, analytics and life-design incubator, bought together global leaders in science, investment, longevity, stem cell research and gene therapy on Sunday.