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uniQure's Investigational Gene Therapy Shows Promising Efficacy With Manageable Safety Risks For Fabry Disease
05 Sep 2025 16:07 GMT
… , an investigational gene therapy for Fabry disease.
Fabry disease is a genetic lysosomal storage … enzyme that breaks down fats.
Fabry disease is caused by a deficiency …
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uniQure Announces Initial AMT-191 Phase I/IIa Data Showing Sustained Increases in α-Gal A Enzyme Activity in Patients with Fabry Disease
05 Sep 2025 11:05 GMT
… Food and Drug Administration. About Fabry Disease Fabry disease is an X-linked genetic … refractory temporal lobe epilepsy, ALS, Fabry disease, and other severe diseases. www … intravenously administered option for treating Fabry disease and the Company’s …
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Sangamo Therapeutics Presents Detailed Data from Registrational STAAR Study in Fabry Disease at International Congress of Inborn Errors of Metabolism 2025
04 Sep 2025 12:05 GMT
… option for people living with Fabry disease.” “Fabry disease is a debilitating and … the underlying pathology of Fabry disease and provide a potentially … infusion without preconditioning. About Fabry Disease
Fabry disease is a lysosomal storage disorder …
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Reimbursement for oral Fabry disease drug Galafold expanded to 1st-line treatment
01 Aug 2025 08:00 GMT
… for this age group.
Fabry disease is a rare, inherited … s first oral treatment for Fabry disease, developed by Amicus Therapeutics … profile in patients with Fabry disease who have a compliant … 9 years, and that Fabry disease-related clinical events occurred …
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Fabry Disease Market Analysis, Key Company Profiles, Product Portfolio, Pipeline Product Analysis, Recent Developments and Dynamics 2025-2030 - ResearchAndMarkets.com
25 Jul 2025 14:37 GMT
… care for managing Fabry disease. The rising prevalence of Fabry disease has directly increased … rare diseases like Fabry disease.
Global Fabry Disease Market Dynamics
Global Fabry Disease Market - Company …
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Sanofi Korea joins hands with DeepCardio to improve diagnostic environment for Fabry disease
24 Jul 2025 06:43 GMT
… diagnostic environment for people with Fabry disease and increase awareness among … enhance the diagnostic environment for Fabry disease, agreeing to launch various initiatives … detection and treatment of undiagnosed Fabry disease patients are of utmost …
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Global Fabry Disease Market Growth, Share & Analysis Report | Emerging Treatments 2025 | DataM Intelligence
02 Jul 2025 13:21 GMT
… companies to focus on Fabry disease therapies.
Market Segmentation:
… v=x5oEiqEqTWg
Conclusion:
The Fabry Disease Market is positioned for … the world.
Related Reports:
Fabry Disease Treatment Market:
Aminoglycosides Market
…
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Fabry Disease Market Size to Reach USD 3,898.0 Million by 2035 - Epidemiology Report by IMARC Group
01 Jul 2025 11:03 GMT
… /fabry-disease-market-report/requestsample
Key Highlights:
Fabry disease affects 1 … The competitive landscape of the Fabry disease market has been studied … AceLink Therapeutics
Buy the full Fabry Disease Treatment Market Epidemiology Report: …
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Galafold confirms effectiveness in treating teens with Fabry disease
25 Jun 2025 08:06 GMT
… that the oral treatment for Fabry disease, Galafold (migalastat), is effective … Handok.
(Courtesy of Handok)
Because Fabry disease is a progressive lysosomal storage … under insurance coverage for treating Fabry disease. However, unlike most countries, Korea …
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Sangamo Therapeutics Announces Positive Topline Results From Registrational STAAR Study in Fabry Disease
24 Jun 2025 12:21 GMT
… with approved treatments for Fabry disease by performing a meta- … safety-related study discontinuations.
“Fabry disease is a debilitating and multifaceted … infusion without preconditioning.
About Fabry Disease
Fabry disease is a lysosomal storage disorder …