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Deklan Locke, whose nickname is Flash, is fighting Duchenne Disease
06 Aug 2025 23:57 GMT
… Flash, has a rare illness, Duchenne muscular dystrophy, which primarily affects boys, … Flash, has a rare illness, Duchenne muscular dystrophy, which primarily affects boys, … , has a rare illness, Duchenne muscular dystrophy, which primarily affects boys, …
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STAT+: Sarepta hired a Trump-connected firm to lobby on Duchenne treatment
06 Aug 2025 23:45 GMT
… over its gene therapy for Duchenne muscular dystrophy, hired a Trump-connected lobbying …
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Hyderabad teen with muscular dystrophy shines at international chess championship
06 Aug 2025 11:51 GMT
… , an 18-year-old battling Duchenne Muscular Dystrophy, competed in the World IPCA … . Praneeth has been bravely battling Duchenne Muscular Dystrophy (DMD), a rare and severe …
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Dyne Therapeutics Announces FDA Breakthrough Therapy Designation for DYNE-251 in Duchenne Muscular Dystrophy (DMD)
04 Aug 2025 11:30 GMT
… treatment of patients with Duchenne muscular dystrophy (DMD), amenable to … -251 in individuals with Duchenne muscular dystrophy (DMD) who have … ) and Duchenne muscular dystrophy (DMD), and preclinical programs for facioscapulohumeral muscular dystrophy (FSHD) …
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Outrage of the Month: Patient Deaths From a Duchenne Muscular Dystrophy Gene Therapy
01 Aug 2025 19:02 GMT
… an approved gene therapy for Duchenne muscular dystrophy linked to three patient deaths … therapy for both types of muscular dystrophy.
Subsequently, the FDA announced … better therapies are needed for Duchenne muscular dystrophy, a rare but devastating genetic …
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Is the tide turning on viral vectors? The shifting landscape of gene therapy delivery
07 Aug 2025 04:42 GMT
… . Furthermore, some diseases such as Duchenne muscular dystrophy (DMD), spinal muscular atrophy, and … for DMD and limb-girdle muscular dystrophy (LGMD). The patients all died …
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Sarepta, with $1B debts due in 2027, weighs efficiency measures
07 Aug 2025 05:13 GMT
… future demand of its flagship Duchenne muscular dystrophy gene therapy Elevidys remains unclear … call in a limb-girdle muscular dystrophy (LGMD) patient who had received …
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Research Tip Sheet: Heart Attack, Muscular Dystrophy, Neuroprosthetics
02 Aug 2025 02:54 GMT
… Therapy Prevents Damage From Duchenne Muscular Dystrophy
A cell therapy preserves muscle … weaker in adults with Duchenne muscular dystrophy. Clinical trials have also … during the natural progression of Duchenne muscular dystrophy.
Other Cedars-Sinai authors …
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Imlifidase enables gene therapy in Duchenne patients with AAV antibodies
04 Aug 2025 12:53 GMT
… and 32% of patients with Duchenne muscular dystrophy (DMD) are unable to receive … , facilitating administration of gene therapy.”
Duchenne muscular dystrophy is a rare and fatal …
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”People Will Pay”: Anti-Vax Voices Rage At Prasad Ouster
07 Aug 2025 01:28 GMT
… over its new treatment for Duchenne Muscular Dystrophy, Elevidys, and was preceded by …