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Duchenne MD Added to Screening Panel; United Spinal Welcomes Hawaii Chapter
22 Dec 2025 22:34 GMT
… ; Human Services (HHS) has added Duchenne muscular dystrophy and metachromatic leukodystrophy to the … when they need them most.”
Duchenne muscular dystrophy typically presents in boys in … . In addition to impacting mobility, Duchenne MD impacts the heart as …
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Capricor Therapeutics, Inc. (CAPR) Discusses HOPE-3 Phase III Trial Results and Regulatory Path for Duchenne Muscular Dystrophy Therapy Transcript
18 Dec 2025 03:27 GMT
… product, deramiocel for treatment of Duchenne muscular dystrophy. I'm Eric Camino …
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HHS Expands Newborn Screening to Include Duchenne Muscular Dystrophy and Metachromatic Leukodystrophy
16 Dec 2025 21:00 GMT
… December 16 the addition of Duchenne Muscular Dystrophy (DMD) and Metachromatic Leukodystrophy (MLD …
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ICYMI: 5 BioSpace Features From 2025 That Stand the Test of Time
23 Dec 2025 05:06 GMT
… of all shipments of the Duchenne muscular dystrophy treatment Elevidys.
When asked how …
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2025 Year in Review: Political Shifts and Policy Battles
22 Dec 2025 22:26 GMT
… December 16 the addition of Duchenne Muscular Dystrophy (DMD) and Metachromatic Leukodystrophy (MLD …
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HHS adds neuromuscular conditions to newborn screening protocol
22 Dec 2025 18:10 GMT
… has announced the addition of Duchenne muscular dystrophy and metachromatic leukodystrophy to the … HHS release, most children with Duchenne muscular dystrophy (DMD) or metachromatic leukodystrophy (MLD …
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2025, the year in pharma: Tariffs, mergers and regulatory volatility
22 Dec 2025 18:27 GMT
… a hold on Sarepta’s Duchenne muscular dystrophy drug for safety concerns.
Susan … of its gene therapy for Duchenne muscular dystrophy to some patients.
Prasad resumes …
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Naughton family looking for famed actor to send message to George
22 Dec 2025 16:31 GMT
… the catastrophic muscle wasting disease, Duchenne Muscular Dystrophy, is presently in hospital but …
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BioSpace Editors’ Top 5 Biggest News Stories of the Year
22 Dec 2025 13:12 GMT
… box warning for its approved Duchenne muscular dystrophy (DMD) gene therapy Elevidys, following …
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Two Neurologic Disorders Added to Newborn Screening Panel
22 Dec 2025 10:47 GMT
… rare congenital neurologic disorders — Duchenne muscular dystrophy (DMD) and metachromatic leukodystrophy … recommend metachromatic leukodystrophy and Duchenne muscular dystrophy for inclusion on … Policy and Advocacy at Muscular Dystrophy Association, said in …