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Duchenne MD Added to Screening Panel; United Spinal Welcomes Hawaii Chapter
22 Dec 2025 22:34 GMT
… (HHS) has added Duchenne muscular dystrophy and metachromatic leukodystrophy to the … children to receive FDA [Food & Drug Administration]-approved therapies … treatment options they deserve — right when they need them most.”
Duchenne muscular dystrophy …
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Prince Louis’ picture hints at Kate Middleton’s life after cancer treatment
21 Dec 2025 16:32 GMT
The 2025 Christmas card that has graced social media via, Prince William and Kate Middleton’s Instagram account is said to encase a ‘secret message’ according to body language expert Chris Pardoe.
He shared these observations on behalf of Online-casinos. …
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Capricor Therapeutics, Inc. (CAPR) Discusses HOPE-3 Phase III Trial Results and Regulatory Path for Duchenne Muscular Dystrophy Therapy Transcript
18 Dec 2025 03:27 GMT
… trial, HOPE-3, which was evaluating their investigational product, deramiocel for treatment … of Duchenne muscular dystrophy. I'm Eric … CEO, Linda Marban, their Chief Medical Officer, Michael Binks; and …
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HHS Expands Newborn Screening to Include Duchenne Muscular Dystrophy and Metachromatic Leukodystrophy
16 Dec 2025 21:00 GMT
… December 16 the addition of Duchenne Muscular Dystrophy (DMD) and Metachromatic Leukodystrophy (MLD … conditions enables children to receive FDA-approved therapies at the most … child’s chances for timely treatment, effective therapies, and, in some …
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Emer Cooke, EMA’s Executive Director: 2025 achievements in medicine regulation
19 Dec 2025 16:31 GMT
… in the European medicines regulatory network’s workforce … age;
the first treatment against Duchenne muscular dystrophy in patients from … of multinational clinical trials taking place in … time information about clinical trials conducted in their area …
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FDA outlined concerns with Elevidys' manufacturing at Catalent site, Form 483 shows
19 Dec 2025 18:29 GMT
… operations were preceded by two FDA inspections in April that resulted … gene therapies including Sarepta Therapeutics’ Duchenne muscular dystrophy therapy Elevidys. While there, inspectors … the manufacturing of a redacted drug product. This time, the agency …
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Columbus is making medical history. It's time the world knew
18 Dec 2025 10:09 GMT
… Duchenne muscular dystrophy.
The high cost of these life-saving treatments … a Boston-based biotech company chooses Columbus … signal.
Columbus doctors are making medical history
Our … worry about sustainability. Drug developers recoup enormous investments …
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Biotech Momentum Carries After-Hours Trading Gains
18 Dec 2025 06:14 GMT
… Health and Human Services added Duchenne muscular dystrophy to the Recommended Uniform Screening … of strength in the biotech sector.
Eledon Pharmaceuticals, Inc. (ELDN) closed at …
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ICYMI: 5 BioSpace Features From 2025 That Stand the Test of Time
23 Dec 2025 05:06 GMT
… on pharmaceutical imports to insisting that drugmakers lower … time, dozens of biotechs are developing next-gen … FDA to request the stoppage of all shipments of the Duchenne muscular dystrophy treatment … as PitchBook Senior Biotech Analyst Kazi Helal put …
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2025 Year in Review: Political Shifts and Policy Battles
22 Dec 2025 22:26 GMT
… federal Centers for Medicare and Medicaid Services (CMS), … 16 the addition of Duchenne Muscular Dystrophy (DMD) and Metachromatic … of Pediatrics (AAP), stating that certain policies … targeting hospitals and doctors offering such treatments.
Congress left …