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Sionna Therapeutics Announces Presentation of SION-719 and SION-451 Phase 1 Data and Poster of New Preclinical Data on the Impact of NBD1 Stabilizers on F508del-CFTR Half-Life at the 2025 North American Cystic Fibrosis Conference
24 Oct 2025 17:15 GMT
… the current treatment paradigm for cystic fibrosis (CF) by developing novel … normalize the function of the cystic fibrosis transmembrane conductance regulator (CFTR) … normalize the function of the cystic fibrosis transmembrane conductance regulator (CFTR) …
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‘Great Strides Walk’ for Cystic Fibrosis canceled due to weather
24 Oct 2025 11:31 GMT
… the Great Strides Walk for Cystic Fibrosis.
Rhonda Kitchens was set to … to find a cure for Cystic Fibrosis on their website HERE.
They …
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Patient groups, supporters form community buyers' club for generic cystic fibrosis drug
24 Oct 2025 11:02 GMT
… lifesaving treatment for cystic fibrosis at the North American Cystic Fibrosis Conference (NACFC) … half BexDeco everyday for children.
Cystic fibrosis is a rare genetic disorder … a life-threatening disease like cystic fibrosis into a manageable condition. …
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STAT+: Advocacy groups form a buyer’s club to obtain generic versions of pricey Vertex cystic fibrosis drug
24 Oct 2025 10:33 GMT
… the price of a lifesaving cystic fibrosis treatment sold by Vertex Pharmaceuticals …
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Vertex Presents New Data Across Portfolio of Cystic Fibrosis Medicines Including ALYFTREK® at the North American Cystic Fibrosis Conference
24 Oct 2025 10:05 GMT
… the Preschool Cystic Fibrosis Questionnaire-Revised in children with cystic fibrosis and … 15 p.m. PDT.
About Cystic Fibrosis
Cystic fibrosis (CF) is a rare, … another responsive mutation in the cystic fibrosis transmembrane conductance regulator (CFTR …
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Living with cystic fibrosis in the bush
24 Oct 2025 06:12 GMT
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Life-changing cystic fibrosis drug Trikafta may get Pharmac funding
23 Oct 2025 23:38 GMT
… news,” said chief executive of Cystic Fibrosis New Zealand, Lisa Burns.
“It …
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Arcturus Plunges on ‘Mixed’ Cystic Fibrosis Data for Inhaled mRNA Drug
23 Oct 2025 15:42 GMT
… improvements in a Phase II cystic fibrosis trial, prompting the biotech … expression and activity of the cystic fibrosis transmembrane conductance (CFTR) regulator … respiratory failure.
Current therapies for cystic fibrosis, such as Vertex Pharmaceuticals’ …
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Arcturus announces mixed results of mRNA cystic fibrosis therapy, Covid-19 vaccine delay
22 Oct 2025 21:29 GMT
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Arcturus Therapeutics Provides Interim Phase 2 Data for Cystic Fibrosis Program
22 Oct 2025 15:19 GMT
… half of 2026. About Cystic Fibrosis Cystic fibrosis is a life-shortening disease … distribution. Mutations in the cystic fibrosis transmembrane conductance regulator (CFTR) … the underlying pathology of cystic fibrosis, the continued clinical development …