… address critical unmet medical needs. A daily pill could make a … migalastat). The drug will soon fall into BioMarin Pharmaceutical’s ownership … 2026, the FDA approved an expanded label for Cerezyme to include … company of the Clinical Trials Arena. Sign up for …

… French pharmaceutical company said Monday. According to Sanofi, the drug, … In a Phase 3 trial, venglustat wasn’t associated … Sanofi sells one called Cerezyme — those treatments don’t help with … to address critical unmet medical needs,” said Houman Ashrafian …

… disease drug venglustat split a pair of Phase III clinical trials, with … in the late-stage LEAP2MONO trial. The drug also matched ERT on … that the Phase III PERIDOT trial did not meet its … well as Cerezyme and Cerdelga for Gaucher. The FDA previously granted …

… and placebo tablet. The trial demonstrated that venglustat met the … also being studied for the treatment of Fabry disease, another … for Fabry disease, and Cerezyme and Cerdelga for Gaucher disease … 2026, the FDA approved an expanded label for Cerezyme to include …

… drugmaker Sanofi said on Monday that its experimental genetic disorder treatment … in ‌a separate trial. The oral drug, venglustat, was … body. Previous failures in trials of patients with Parkinson … disease, and markets Cerezyme and the oral drug Cerdelga for ‌ …

… the new trial showed that a daily dose of the drug achieved … (ERT) for Gaucher disease. The drug also improved non-neurological symptoms … a 'pipeline-in-a-pill' candidate with big sales … ;s type 1 and 3 treatment Cerezyme (imiglucerase), there are a …

… address critical unmet medical needs. A daily pill could make … reported adverse events during treatment among patients receiving venglustat … an expanded label for Cerezyme to include non-central … US Food & Drug Administration (FDA) for its potential use …

… 'indication aux États-Unis, Cerezyme peut désormais être prescrit à … accélérée dela Food & Drug Administration (FDA) américaine pour son utilisation potentielle … demande d’autorisation concernant un médicament, dispositif ou produit biologique, ainsi …

… ’s Cerezyme has long been used as a treatment for Gaucher … that clinical trial results showed its experimental oral drug venglustat improved … now plans to submit the drug to regulators.  “For many … amp;D, referring to drugs like Cerezyme that work by effectively …

… ITP in the EU, Cerezyme for Gaucher disease Type 3 … commitment to bringing innovative medicines and treatments to Chinese patients and … cost versus building your drug pipeline? And then perhaps … by interactions with the FDA predominantly to establish exactly …