Bleeding Disorders (incl. Hemophilia, Von Willebrand Disease) Newsletter
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Gene Therapy Cuts Bleeding and Medicine for Hemophilia B Patients for Over a Decade
17 Jun 2025 23:37 GMT
… protein missing in people with hemophilia B. This reduces bleeding … about 7,000 individuals have hemophilia B, according to a … study of Hemophilia Treatment Center (HTC) patients … bleeding and medication needs in hemophilia B patients in the …
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This Week’s CGT News: Investigating the Long-Term Safety of Gene Therapy for Hemophilia B
17 Jun 2025 16:29 GMT
… safety of gene therapy for hemophilia B
A 13-year follow … efficacy of gene therapy for hemophilia B. Ten adults with severe … available for gene therapy in hemophilia B, offering critical evidence for …
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Case Study Uncovers Potential Autoimmune Link Between Hemophilia A and Primary Biliary Cholangitis
14 Jun 2025 03:07 GMT
… possible link between acquired hemophilia A, a life-threatening … medical connection between acquired hemophilia A (HA) and … Factor VIII.
Unlike inherited hemophilia, acquired HA typically appears … had no history of bleeding disorders or recent medication use. …
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Gene therapy offers long-term relief for Haemophilia B: Study
13 Jun 2025 20:03 GMT
… time gene therapy approach for haemophilia B remains safe and … , confirming its enduring benefits.
Haemophilia B, an X-linked genetic … adult males with severe haemophilia B received a one-time … a transformative shift in how haemophilia B is treated, offering …
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Hemophilia B Gene Therapy Demonstrates Long-Term Success
13 Jun 2025 08:41 GMT
… treating the bleeding disorder hemophilia B remains safe and … factor IX. Treatment for hemophilia B has traditionally been expensive … 10 adults with severe hemophilia B who received the … Foundation of Memphis, the Hemophilia of Georgia Foundation, the …
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Half of Severe Hemophilia A Cases Have No Family History, Delaying Diagnosis but Not Raising Inhibitor Risk
13 Jun 2025 04:49 GMT
… half of patients with severe hemophilia A (HA) had no … a new study published in Haemophilia.
HA is an inherited … 5,600 male births, while hemophilia B is less common, … particularly in families with unknown hemophilia history, could help identify carriers …
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Gene therapy shows long-term success in hemophilia B patients
13 Jun 2025 03:50 GMT
… to treating the bleeding disorder hemophilia B remains safe and … for any gene therapy for hemophilia B. The results, including … factor IX. Treatment for hemophilia B has traditionally been expensive … 10 adults with severe hemophilia B who received the …
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Mountain States & Southwest Industry News: June 2025
16 Jun 2025 16:03 GMT
… charities, Ryan House and Arizona Bleeding Disorders, as charitable partners for the … hands-on project with Arizona Bleeding Disorders.
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CSL (ASX:CSL) Strengthens Its Footing in S&P/ASX 200 Healthcare Space
16 Jun 2025 08:27 GMT
… serious medical conditions such as bleeding disorders, immune deficiencies, and hereditary angioedema …
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Hundreds line Ardmore’s Lancaster Avenue to protest Trump administration
15 Jun 2025 01:08 GMT
… as a member of the bleeding disorders community, a group that he …
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