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<![CDATA[Vamorolone and Prednisolone Combination Appears Safe in Gene Therapy–Treated Patients With Duchenne]]>
11 Oct 2025 05:09 GMT
… ) and prednisolone while on microdystrophin gene therapy did not lead to any … progression. Because gene therapy doesn’t immediately halt inflammation or muscle breakdown, continuing … safe and equitable use of gene therapy in DMD. The recommendations, which …
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Dr Jitendra lauds Christian Medical College Vellore for successful Haemophilia gene therapy
11 Oct 2025 01:53 GMT
… , the 10th Annual “Cell and Gene Therapy” Symposium organised by the Centre … India’s first-in-human gene therapy trial for Hemophilia A. The … , and quality healthcare, whether physical or mental, is essential for building …
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Sex Differences in Pig Blood Gene Expression
11 Oct 2025 03:56 GMT
… study published in BMC Genomics, researchers led by Lin … linked to disease resistance or growth rate are more … and application in animal genetics. This work underscores the … agricultural biotechnology.
Tags: bioinformatics in gene analysisblood as a biological …
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New therapy 'fixes' genes tied to brain disorders... reversing symptoms of debilitating diseases suffered by millions
11 Oct 2025 05:01 GMT
… diseases where a gene is completely missing or where a single … symptoms using antiseizure medications or implanting devices into the … cannot be blamed on genetics alone and is likely … the first evidence that... gene therapy can restore SYNGAP1 function and …
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A blood test breakthrough for detecting heart damage from cancer therapy
10 Oct 2025 23:56 GMT
… checkpoint inhibitors, or ICIs, have revolutionized cancer therapy, yet their use … cell type-specific profiling of gene expression. This is not … cell-specific changes in gene expression can allow the … to discriminate changes in gene expression due to ICI- …
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New gene therapy restores brain function in SYNGAP1 disorder
10 Oct 2025 17:22 GMT
… have designed a new gene therapy that successfully reversed symptoms … diseases where a gene is completely missing or where a … single copy of a gene is … dramatic improvements – suggesting that gene therapy could remain effective even after …
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Shape Therapeutics Shares Breakthrough Preclinical Data for Non-Invasive Treatment of Parkinson’s Disease Using a Brain Targeted AAV Gene Therapy at the European Society of Gene & Cell Therapy 32nd Annual Congress
10 Oct 2025 10:00 GMT
… ’s novel RNAfix® gene therapy enables targeted knockdown of … major barriers in neurological gene therapy: poor blood-brain … No approved disease slowing or modifying treatments exist … gene therapy industry. Alongside the company’s own RNA-targeting gene therapy …
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Advances in the Drug Delivery Systems for Psoriasis Topical Therapy
10 Oct 2025 17:49 GMT
… keratolytics can alleviate inflammatory cytokines or inhibit immune activation, thereby … offer potential for monotherapy or adjunctive therapy conversion, particularly for patients … protein delivery and CRISPR-Cas9 gene therapy of inflammatory skin disorders. …
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The one therapy proven to protect a person’s joints and ease pain
10 Oct 2025 18:00 GMT
… being guided toward the one therapy proven to protect their … are referred to exercise or physiotherapy by their primary … as:
swelling
tenderness
grating or crackling sound when moving the … cell damage and even altering gene expression.
Exercise first, surgery …
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VRK2 Targeting Boosts Anti-PD-1 Therapy via MYC
10 Oct 2025 18:00 GMT
… HCC patients display intrinsic or acquired resistance to these therapies … techniques, including CRISPR-Cas9-mediated gene editing, quantitative proteomics, and …
Tags: anti-PD-1 therapy enhancementhepatocellular carcinoma treatmentimmune checkpoint blockade …