… Becca Whitmer, who lives with Rett syndrome. Earlier this year, with help …

… editing of MECP2 to rescue Rett syndrome neurons. Sci Transl Med. 2023 …

… uses a wheelchair due to Rett syndrome, a neurological disorder. Although it …

… for oral solution, to treat Rett syndrome. Rett syndrome is a rare neurodevelopmental disorder … with Daybue oral solution in Rett syndrome patients. Findings from a bioequivalence … and only approved treatment for Rett syndrome, has provided thousands of …

… children and adults living with Rett syndrome new flexibility and choice regarding … and only approved treatment for Rett syndrome, has provided thousands of patients … Trofinetide for the Treatment of Rett Syndrome. December 12, 2025. Accessed December …

… only FDA-approved treatments for Rett syndrome, a rare neurodevelopmental disorder … formulation will remain available. About Rett Syndrome Rett syndrome is a rare, complex, … al. Consensus guidelines on managing Rett syndrome across the lifespan. BMJ …

… RVL-001 clinical trials for Rett syndrome (“RTT”) and Pitt Hopkins syndrome …

… the hospital. Michaela, who has Rett syndrome, is a beneficiary of the … of Marie Wohlers) Michaela has Rett syndrome, a rare genetic neurological disorder …

… inherited mutations that lead to Rett syndrome, a rare neurodevelopmental disorder. … unmet medical need.” About Rett Syndrome Rett syndrome is a rare genetic neurodevelopmental … clock care. About Rett Syndrome Research Trust The Rett Syndrome Research Trust is …

… gene therapy for females with Rett syndrome. The study included subjects aged … -in-class gene therapy for Rett syndrome. “It is gratifying to see … across key clinical areas of Rett syndrome, including ambulation and gross motor …