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Germany will be first launch for PTC's phenylketonuria drug
25 Jun 2025 15:28 GMT
… ; treatment for the rare disease phenylketonuria (PKU), Sephience, setting up a …
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PTC Therapeutics’ Sephience gets European marketing authorization to treat children and adults living with phenylketonuria
24 Jun 2025 08:38 GMT
… children and adults living with phenylketonuria (PKU). The authorization includes a … adult and pediatric patients with phenylketonuria (PKU). Sephience is a natural … drug in the United States.
Phenylketonuria (PKU) is a rare, inherited …
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Sephience™ (sepiapterin) Granted Marketing Authorization by the European Commission for the Treatment of Children and Adults Living with Phenylketonuria (PKU)
23 Jun 2025 12:16 GMT
… children and adults living with phenylketonuria (PKU). The authorization includes a … adult and pediatric patients with phenylketonuria (PKU). Sephience is a natural … in the United States.
About Phenylketonuria
Phenylketonuria (PKU) is a rare, inherited …
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Fast Five Quiz: Infant Phenylketonuria
19 Jun 2025 16:32 GMT
A rare disorder, phenylketonuria (PKU) affects how patients process …
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Phenylketonuria (PKU): Market View: 262 Molecules In The Pipeline With 18 Assets Nearing Market
18 Jun 2025 10:10 GMT
… GlobeNewsWire - Nasdaq) Explore the Phenylketonuria Therapeutics market with our comprehensive … and future competitive landscape in Phenylketonuria (PKU) Therapeutics. In 2024 … trends shaping and driving the Phenylketonuria Therapeutics market. Drive revenues …
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Phenylketonuria Therapeutic at a Turning Point as Gene Therapy and Small Molecules Challenge Incumbents | CI Insights
30 May 2025 12:29 GMT
… ;strategic-insights/ci/phenylketonuria-pku
However, competitive pressure is … ;strategic-insights/sample/phenylketonuria-pku
To stay ahead, pharmaceutical … ?
Our comprehensive CI report on Phenylketonuria offers an in-depth view …
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Phenylketonuria Clinical Trial Pipeline Appears Robust With 25+ Key Pharma Companies Actively Working in the Therapeutics Segment | DelveInsight | DelveInsight
29 Apr 2025 17:00 GMT
… recent advances in phenylketonuria drugs @ Phenylketonuria Pipeline Report The phenylketonuria pipeline report … the emerging phenylketonuria therapies @ Phenylketonuria Clinical Trials Phenylketonuria Therapeutics Assessment The phenylketonuria pipeline …
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Cycle Pharmaceuticals Launches Cycle Vita PKU™, an AI-Powered Smartphone App for On-The-Go Management of Phenylketonuria (PKU)
22 Apr 2025 14:03 GMT
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National Institutes of Health. 2024. Phenylketonuria (PKU). Available at: https:… do health care providers diagnose phenylketonuria (PKU)? Available at: https:… . What are common treatments for phenylketonuria (PKU)? Available at: https:…
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Phenylketonuria as an Adherence Disease
12 Apr 2025 16:27 GMT
… childhood in individuals with phenylketonuria: early signs of treatment … children with moderate hyperphenylalaninemia and phenylketonuria: a prospective study. Orphanet … Fluctuations in phenylalanine concentrations in phenylketonuria: a review of possible …
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BioMarin Pharma’s phase 3 PEGASUS trial evaluating Palynziq in adolescents with phenylketonuria meets primary efficacy endpoint
03 Apr 2025 13:20 GMT
… adolescents aged 12-17 with phenylketonuria (PKU) compared to diet alone … adolescents aged 12-17 with phenylketonuria. The primary endpoints are change … levels in adult patients with phenylketonuria who have uncontrolled blood Phe …
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