In this episode, Carol Wittlieb-Weber, MD, provides cardiology context for why vamorolone’s pharmacologic profile is generating interest beyond skeletal muscle outcomes. She explains the role of aldosterone and mineralocorticoid receptor signaling in heart …

Physical symptoms can include delayed motor milestones, a waddling gait, enlarged calf muscles, trouble rising from the floor, and eventually heart and breathing complications. For Wilson, who lives in Gate Pā, leaving her house and returning to her …

Duchenne muscular dystrophy (DMD) follows a predictable trajectory …

Duchenne muscular dystrophy (DMD) is a severe, X- …

… in his second attempt. Battling muscular dystrophy since birth, Singla proved that … , Singla spoke about living with muscular dystrophy, a genetic disorder in which …

… Dead surprised kids at the Muscular Dystrophy Association’s annual Christmas party … Marin-Sonoma chapter of the Muscular Dystrophy Association. Per journalist Steve McNamara … two electric sets. For the muscular dystrophy show, the Grateful Dead stuck …

… Welby, a sufferer of progressive muscular dystrophy, to suspend treatment. The court …

… 16 the addition of Duchenne Muscular Dystrophy (DMD) and Metachromatic Leukodystrophy (MLD …

… applying. Cerebral palsy, autism and muscular dystrophy are the most frequent diagnoses …

… associated with myotonic dystrophy, a genetic disorder that causes muscular dystrophy. Some studies … nearly all patients with myotonic dystrophy type 1, which suggests it …