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Dubai hospital aims to be 'global hub' for new spinal muscular atrophy treatment
25 Dec 2025 03:44 GMT
… gene-therapy treatment for spinal muscular atrophy.
Medcare Royal Specialty Hospital in … Itvisma, to patients with spinal muscular atrophy or SMA who are aged …
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UAE-approved drug offers hope to older children with spinal muscular atrophy
23 Dec 2025 06:34 GMT
A new spinal muscular atrophy (SMA) drug approved in the …
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The Emirates Drug Foundation approves gene therapy for gene replacement in a new age group of spinal muscular atrophy patients.
22 Dec 2025 08:13 GMT
… genetic diseases such as spinal muscular atrophy. This decision demonstrates the … treatment, giving individuals with spinal muscular atrophy (SMA) who were previously … extensive experience in treating spinal muscular atrophy and multiple sclerosis, and …
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Confined to a Cuban hospital: When electricity is a matter of life or death
28 Dec 2025 05:38 GMT
… patient with type 1 spinal muscular atrophy — also known as Werdnig-Hoffmann … she has some type of muscular atrophy.
Her grandfather has only been … had been diagnosed with spinal muscular atrophy type 1, a condition that …
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Fatal Complication of Stem Cell Transplants Gets Its First FDA-Approved Therapy
26 Dec 2025 21:59 GMT
… Novartis gene therapy for spinal muscular atrophy initially approved in 2019 for …
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US deportations of Polish citizens almost double this year amid Trump clampdown
26 Dec 2025 14:35 GMT
… of whom suffer from spinal muscular atrophy, have now decided to move …
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Woo! Science: RNA rocks, and UMass Professor Ryder's written the book
26 Dec 2025 10:33 GMT
… neurological diseases such as spinal muscular atrophy
interference RNA therapeutics, which have …
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Precision medicine in the UAE is set to change lives
26 Dec 2025 07:02 GMT
… . For families confronted by spinal muscular atrophy – a rare but debilitating genetic …
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Indian parents are in a new race. Turning children into book authors is the new black belt
26 Dec 2025 06:36 GMT
… Keya Hatkar, who has spinal muscular atrophy, received the Pradhan Mantri Rashtriya …
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EditorialPrecision medicine in the UAE is set to change lives
26 Dec 2025 04:38 GMT
… . For families confronted by spinal muscular atrophy – a rare but debilitating genetic …