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Capricor Therapeutics Announces Positive Type-B Meeting with FDA for CAP-1002 Program for Duchenne Muscular Dystrophy
24 Apr 2024 13:00 GMT
… asset CAP-1002 in treating Duchenne muscular dystrophy (“DMD”). The FDA has affirmed … development for the treatment of Duchenne muscular dystrophy (DMD). Capricor is also harnessing …
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DeWine Announces Ohio First State in the Nation to Screen Newborn Babies for Duchenne Muscular Dystrophy
23 Apr 2024 22:00 GMT
… screening all newborn babies for Duchenne Muscular Dystrophy (DMD).
The provision was … the country to screen for Duchenne Muscular Dystrophy (DMD) in newborns,” said … as Certified Duchenne Care Centers by the Parent Project Muscular Dystrophy advocacy …
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First in the nation, Ohio to start screening newborns for Duchenne muscular dystrophy
23 Apr 2024 18:02 GMT
… the country to screen for Duchenne muscular dystrophy (DMD) in newborns,” said … to begin screening newborns for Duchenne muscular dystrophy was included in H.R … as Certified Duchenne Care Centers by the Parent Project Muscular Dystrophy advocacy organization …
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First Clinical Trial Results of Gene Therapy (GNT0004) for Duchenne Muscular Dystrophy Presented at International Myology 2024 Congress
23 Apr 2024 17:00 GMT
… gene therapy trial for Duchenne Muscular Dystrophy with GNT0004 product, … gene therapy trials for Duchenne muscular dystrophy.
Following the positive … of Myology (Paris).
About Duchenne muscular dystrophy
Duchenne muscular dystrophy is a rare, progressive, …
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Duchenne UK and Parent Project Muscular Dystrophy Award $500,000 to Evaluate Safety and Tolerability of Muscle Progenitor Cells in Phase 1 Trial
23 Apr 2024 18:30 GMT
… organizations dedicated to ending Duchenne muscular dystrophy (Duchenne), are excited to announce … muscle progenitor cells for Duchenne muscular dystrophy.
In response to the … quot;
ABOUT PARENT PROJECT MUSCULAR DYSTROPHY
Duchenne is a genetic disorder …
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Ohio becomes 1st state to screen newborns for Duchenne Muscular Dystrophy
22 Apr 2024 20:42 GMT
… to begin screening newborns for Duchenne Muscular Dystrophy, Gov. Mike DeWine announced Monday … by DeWine in July 2023. Duchenne Muscular Dystrophy (DMD) was added to a … the country to screen for Duchenne Muscular Dystrophy in newborns,” said DeWine. “ …
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Opinion: An FDA pathway can accelerate innovation for Duchenne muscular dystrophy
22 Apr 2024 11:48 GMT
… with innovation.
Charlie has Duchenne muscular dystrophy, a degenerative genetic disease … was a pathway for Duchenne therapies, providing children like … broadly available therapies for Duchenne? Eteplirsen was just the … a cure for Duchenne muscular dystrophy.
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Edgewise Receives European Medicines Agency (EMA) Orphan Drug Designations for Sevasemten (EDG-5506) for the Treatment of Becker and Duchenne Muscular Dystrophies
23 Apr 2024 12:15 GMT
… of Becker muscular dystrophy (Becker) and for the treatment of Duchenne muscular dystrophy (Duchenne). Sevasemten is … ;/beckermusculardystrophy.com/
About Duchenne Muscular Dystrophy
Duchenne is a severe, degenerative muscle …
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What is DMD? Gov. DeWine announces Ohio to screen newborns for disease
24 Apr 2024 11:53 GMT
… newborns for a disease called Duchenne Muscular Dystrophy (DMD).
“Adding DMD to the … Ohio each year.
What is Duchenne Muscular Dystrophy (DMD)?
DMD is a hereditary … most severe forms of inherited muscular dystrophy, according to the Ohio Department …
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Sarepta Therapeutics to Announce First Quarter 2024 Financial Results
24 Apr 2024 12:44 GMT
… . We hold leadership positions in Duchenne muscular dystrophy (DMD) and limb-girdle muscular …