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Terminal breast cancer patients denied life-extending drugs - report
01 Jul 2025 23:36 GMT
… medication due to an "unfair" assessment process for NHS drug … example to treatments for cystic fibrosis, hepatitis D and Duchenne muscular dystrophy – and has … for cancer medicines and non-cancer medicines.
“And other breast cancer treatments have …
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Breast cancer patients ‘denied life-extending drugs because of unfair system’
01 Jul 2025 23:09 GMT
… could be denied life-extending drugs because of the “unfair” way … example to treatments for cystic fibrosis, hepatitis D and Duchenne muscular dystrophy – and has … to supporting the introduction of medicines at a cost-effective price …
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FDA Activity Recap: June 2025 Features New Platform Designation, IND Clearance, and More
01 Jul 2025 21:12 GMT
… 47;2 ascending-dose clinical trial. Nuevocor expects to launch the … treatment of Duchenne muscular dystrophy (DMD) cardiomyopathy, is not currently required.
The Prescription Drug … 25, 2025 — The FDA has granted regenerative medicine advanced therapy (RMAT) …
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FDA Grants Platform Technology Designation to Limb-Girdle Muscular Dystrophy Gene Therapy Vector
01 Jul 2025 02:55 GMT
… support of investigational new drug applications and biologic … an FDA-approved gene therapy intended to treat Duchenne muscular dystrophy (DMD … phase 3 EMERGENE clinical trial (NCT06246513).3 Safety … for the treatment of limb girdle muscular dystrophy type 2E…
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AI-Based Electrocardiogram Interpretation Detects LVSD in Muscular Dystrophy
01 Jul 2025 02:55 GMT
… in muscular dystrophies, including Duchenne muscular dystrophy (DMD), in which … at the University Medical Center Utrecht hospital … and initiation of cardioprotective treatment are crucial. Therefore, … studies and cluster randomized trials, they added. Their …
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Duchenne Muscular Dystrophy (DMD) Market Size in the 7MM to Reach USD 3,906.1 Million by 2035
30 Jun 2025 16:29 GMT
… treatment … Duchenne muscular dystrophy marketed drugs and late-stage pipeline drugs.
In-Market Drugs
Drug … Overview
Mechanism of Action
Regulatory Status
Clinical Trial Results
Drug … Pharmaceuticals…
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Becker Agent Sevasemten Shows Long-Term Treatment Effects in Latest Extension Data
01 Jul 2025 13:07 GMT
… 2 LYNX and FOX trials of Duchenne muscular dystrophy (DMD), as well … be consistent with the drug remaining favorable among treated … , MD, PhD, chief medical officer at Edgewise, said in … 12-month treatment period.2 Following the trial, Edgewise completed …
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Improving RNA drug delivery through intracellular traffic control
01 Jul 2025 07:27 GMT
… transport of RNA-based drugs can significantly enhance their … medicine, personalized therapies are becoming increasingly important – particularly in the treatment … ALS) and Duchenne muscular dystrophy.
Limited efficacy of RNA-based drugs
A key challenge …
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Student with Duchenne Muscular Dystrophy Finding a Home at VPCC's Historic Triangle Campus
29 Jun 2025 18:50 GMT
… — Since Nicholas Bahl-Moore has Duchenne muscular dystrophy, he and his family had … in the last 50 years, Duchenne has made some strides with … responsibility.
“We’re advocating about Duchenne, and learning and understanding it …
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People with disabilities fear loss of coverage as new Medicaid rules take effect
30 Jun 2025 22:44 GMT
… life functions.
Jacobs, 24, has Duchenne muscular dystrophy and has used a wheelchair … heart medications as well as drugs to mitigate the effects of his muscular dystrophy … .
“If I don’t remember to take certain medicines, it …