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ReCode Therapeutics Initiates Enrollment of Phase 2 Clinical Trial of RCT2100 in Combination with Ivacaftor for the Treatment of Cystic Fibrosis
18 Nov 2025 12:58 GMT
… .S. Food and Drug Administration (FDA) has granted clearance … ongoing Phase 2 clinical trial evaluating RCT2100, an … in the lungs.
About Cystic Fibrosis
Cystic fibrosis (CF) is a progressive, serious … treatment of the 10% to 15% of people with cystic fibrosis …
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ReCode initiates Phase II trial of RCT2100 with ivacaftor for CF
18 Nov 2025 11:12 GMT
… II clinical trial of the inhaled cystic fibrosis transmembrane conductance … combined with ivacaftor for cystic fibrosis (CF).
This stage of the … the US Food and Drug Administration (FDA), with clinical sites … multi-part Phase II trial will assess RCT2100’s …
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New Nasal Test Promising for Children With Cystic Fibrosis
18 Nov 2025 06:54 GMT
… Translational Medicine, Regional Centre of Cystic fibrosis — University of Naples “Federico II … marker of disease progression or treatment response over time. Validation of … expert board meetings for multiple pharmaceutical companies.
This article was created …
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Analysis of the Results of Monitoring the Quality of Services in Oncological Treatment, Conducted as Part of the Pilot Project of the National Cancer Network for Lung Cancer in 2019-2023, in Poland
17 Nov 2025 03:53 GMT
… information from the treating physician about the treatment process, for … AL, Siegel S, Kirstein CF, et al. Measuring patient … development and implementation. J Med Internet Res. 2018; … and colorectal cancer treatment: a randomized trial. Cancer Epidemiol …
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Elexacaftor/Tezacaftor/Ivacaftor Benefits Kids with CF
15 Nov 2025 07:20 GMT
Cystic fibrosis (CF), a debilitating genetic … the potential of early pharmacological intervention to preserve … future for early-stage CF treatment, it also raises … cystic fibrosis alone; it exemplifies how understanding molecular pathophysiology can drive drug …
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Vast Therapeutics Completes First Milestone in Phase 1 Clinical Program
18 Nov 2025 12:28 GMT
… ALX1 drug candidate which evaluated safety, tolerability and pharmacokinetics in … an open Investigational New Drug application with the U … rare orphan diseases like cystic fibrosis (CF) to adults with the … disease (COPD). Our drug candidates target the nitric …
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Walberg opens Farrell drug store in era of other pharmacy store closures
15 Nov 2025 02:09 GMT
FARRELL – A new pharmacy in Farrell opened its doors … have seen drug stores permanently close.
Walberg Family Pharmacies bought Valley Pharmacy which … E96:C AC6D4C:AE:@?D CF?D @FE 2?5 2D … :G6 52JD 367@C6 E96J CF? @FE]k^Am
kAm%96 AC …
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<![CDATA[US Spending on High-Revenue Rare Disease Drugs in 2022]]>
14 Nov 2025 18:56 GMT
… clinical trial costs for developing drugs to treat … drugs with Orphan Drug Act designations generate similar sales to drugs treating … cystic fibrosis. In some cases, patients with these conditions had limited treatment … of expensive medications.43
CONCLUSION
…
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Editorial: The FDA’s meltdown escalates
14 Nov 2025 20:49 GMT
The Food and Drug Administration shouldn’t be in … . There are currently no approved drugs that can slow progression of … ,000 Americans. The FDA in April designated UniQure’s treatment a “breakthrough … ;FC6 >:89E 92G6 E@ CF? 2?@E96C EC:2= H …
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Guest editorial | FDA has been an embarrassment in Trump's second term
14 Nov 2025 14:30 GMT
… Tribune-Democrat.
The Food and Drug Administration shouldn’t be in … right. By that measure, the FDA is failing in spectacular fashion … ;FC6 >:89E 92G6 E@ CF? 2?@E96C EC:2= H …