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Long Island boy, 8, is first in NYS to receive new therapy for blood disorder
19 Apr 2024 15:27 GMT
An 8-year-old Long Island boy born with a genetic blood condition was the first person in New York to receive a “promising” treatment that has so far enabled him to stop the frequent blood transfusions vital to keeping him healthy.
Yusef Saeed, of Valley …
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Boy with rare blood disorder receives new life-changing gene therapy treatment
19 Apr 2024 02:05 GMT
… to undergo gene therapy treatment for a rare … with a rare genetic blood disorder called thalassemia. This means … quot;Historically, the only treatments were medical management with chronic … approved and transformative gene therapy treatment. Dr. Banu Aygun, …
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Long Island boy with rare blood disorder undergoes gene therapy
18 Apr 2024 23:39 GMT
… (PIX11) — Until now, the best treatment for some diseases has been … was born with a rare blood disorder known as beta thalassemia which … the patient’s cells for treatment.
Dr. Banu Aygun, the … in the making, this new treatment marks a major medical milestone …
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8-year-old boy first in NY to receive FDA-approved gene therapy for rare inherited blood disorder
18 Apr 2024 21:02 GMT
… therapy for a rare inherited blood disorder called beta-thalassemia.
"Speaking … Medical Center.
Previously, the only treatment options were a bone marrow … , you know, get him to treatment. So and we're …
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Press Release: Rilzabrutinib LUNA 3 phase 3 study met primary endpoint in immune thrombocytopenia
23 Apr 2024 05:00 GMT
… of next-generation transformative treatments for immune diseases
… Food and Drug Administration (FDA) for the treatment of … and expertise in rare blood diseases and ability to … serious, acquired autoimmune blood disorder characterized by autoantibody-mediated …
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Selective Inhibitor of Spleen Tyrosine Kinase Discovered
23 Apr 2024 04:55 GMT
… be useful for the treatment of such diseases. Existing … while retaining the necessary drug-like properties (e.g … ., metabolic stability). The drug candidates promising properties were … purpura (ITP, a blood disorder), warm antibody autoimmune hemolytic …
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Cohen Children’s Medical Center Performs First Gene Therapy Treatment For Thalassemia in NYS
19 Apr 2024 16:22 GMT
… to recognize the groundbreaking treatment on the young patient, … is a rare, genetic blood disease caused by mutations in the … gene therapy treatment. In the first pre-treatment phase, the … training to administer this treatment.
While Yusef played happily …
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7 Asian Americans whose discoveries changed the world
22 Apr 2024 20:14 GMT
… getting cutting-edge products and treatments into peoples' hands … needed to take HIV medications and did not exhibit … by giving them anti-HIV drugs hours after birth.
In … scientists to understand and treat blood disorders.
Lujendra Ojha
Lujendra Ojha, …
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It's time to return the serve on extreme Rx pricing
22 Apr 2024 15:11 GMT
… .
As specialty drugs, treatments and prescription medications continue to increase … struggling to afford essential medications that fight infection, … lowest drug prices
Others may have treatments that … to treat a genetic blood disorder, helped prevent blood …
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ARH to build new $15m cancer centre in Kentucky, US
22 Apr 2024 11:10 GMT
… neighbouring areas to receive cancer treatment closer to their home, without … illnesses, such as chronic leukaemia, blood disorders, lymphoma, cancer, myelodysplasia, and multiple …