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QUB Announces New £12m Rare Disease Research Centre
25 Apr 2024 15:24 GMT
… trials for rare diseases.
The LifeArc Centre for Acceleration of Rare Disease Trials … people living with rare diseases. However, clinical trials for rare diseases are challenging … , and increasing participation in rare disease research are key priorities for …
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PM Modi Receives Special Letter From Father of Child Suffering From Rare Disease Duchene Muscular Dystrophy, Appeals for Financial Assistance
25 Apr 2024 17:13 GMT
… , who is suffering from a rare disease, Mohammad Fazal Yaseen Kidwai, a …
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Brave face: Marlborough girl, 11, with rare disease a star on TikTok
25 Apr 2024 17:14 GMT
MARLBOROUGH — Vitoria Bueno says she’s a little shy, but you wouldn’t know it by her online presence.
Vitoria is a TikTok star at age 11, with 1.2 million followers and counting. Her handle, @grwms.by.vitoria, gives fans a steady supply of tips on how to …
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Scottish mum heartbroken as newborn diagnosed with rare disease needs urgent transplant
25 Apr 2024 13:38 GMT
… baby was diagnosed with a rare disease and is now in desperate …
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Esteve Healthcare To Buy Perrigo's HRA Pharma Rare Diseases Business For Up To EUR 275 Mln
25 Apr 2024 11:09 GMT
… Perrigo's HRA Pharma Rare Diseases business for up to 275 … 85 million euros on the Rare Diseases business achieving certain sales milestones … .
"Divesting the HRA Pharma Rare Diseases business further supports our position …
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STAT+: Why a British hospital, and not a drugmaker, is trying to get a rare disease therapy approved
25 Apr 2024 09:57 GMT
… promising genetic therapies for ultra-rare diseases or halted their research programs …
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Mum heartbroken after tiny newborn baby placed on transplant list after being diagnosed with rare disease
25 Apr 2024 03:42 GMT
The mum of a tiny baby on the transplant list is desperately hoping a donor will be found to save her little girl's life. Five-month-old Helin Dinler now needs a liver donor or she will not see her second birthday. The newborn was diagnosed with …
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Denise D’Ascenzo foundation’s walk for rare diseases raising money for local charities, including ALS United CT
24 Apr 2024 21:57 GMT
… ’Ascenzo Foundation’s walk for rare diseases.
Money raised will help a … D’Ascenzo foundation walk for rare diseases. The walk is this Saturday …
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Neurocrine launches CAH rare disease education campaign ahead of FDA submission
24 Apr 2024 20:57 GMT
Neurocrine Biosciences’ newly-debuted campaign acknowledges the frustration that congenital adrenal hyperplasia (CAH) patients, families and endocrinologists often feel.
The “What the C@H?!” theme is a tongue-in-cheek play on the …
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Chiesi Global Rare Diseases Announces Publication of Results from Fabry Disease Patient Survey
24 Apr 2024 18:40 GMT
… the numerous unique challenges that rare disease patients face every day, … quot;
About Chiesi Global Rare Diseases
Chiesi Global Rare Diseases is a business unit … therapeutic solutions in respiratory health, rare diseases, and specialty care. The company …