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'You can start treatments right away'; Arizona family pushes to get all newborns screened for deadly muscular dystrophy
19 Apr 2024 12:48 GMT
… Duchenne muscular dystrophy to the screening process.
Anthony Castle, 24, has Duchenne muscular dystrophy, … got the diagnosis of Duchenne muscular dystrophy.”
Jill was told Anthony … future families dealing with Duchenne muscular dystrophy have one less …
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Parent Project Muscular Dystrophy Launches First State-Specific Duchenne Advocacy Day in Illinois
17 Apr 2024 07:35 GMT
… leading the fight to end Duchenne muscular dystrophy (Duchenne), is proud to announce … September 7, 2024, as Duchenne Muscular Dystrophy Awareness Day in the State … website.
ABOUT PARENT PROJECT MUSCULAR DYSTROPHY
Duchenne is a genetic disorder that …
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Edgewise reports data from trial of muscular dystrophy drug
16 Apr 2024 13:00 GMT
… 5506) in adults with Becker muscular dystrophy.
Sevasemten is an orally … dystrophinopathies such as Becker and Duchenne muscular dystrophy.
The open-label, single- … 12 adult males with Becker muscular dystrophy, who were administered sevasemten daily …
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Edgewise Therapeutics Announces Positive Two-Year Topline Results from the ARCH Open Label Trial of Sevasemten (EDG-5506) in Adults with Becker Muscular Dystrophy (Becker)
15 Apr 2024 20:10 GMT
… dystrophinopathies including Becker and Duchenne muscular dystrophy (Duchenne).
This press release … Functional changes in Becker muscular dystrophy: implications for clinical trials … in adults with Becker muscular dystrophy: disease progression detected …
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Inspired by idol Messi, S’porean soccer player, 23, strives to dribble & feint like him but in a wheelchair
19 Apr 2024 11:51 GMT
… sportsman Tan was diagnosed with Duchenne Muscular Dystrophy (DMD) when he was just … .
He was introduced by the Muscular Dystrophy Association (MDAS) to power soccer …
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Venture 50: Early-stage research & development draw investors to clean tech & life sciences sector
18 Apr 2024 22:47 GMT
… in its potential to treat Duchenne muscular dystrophy.
That confidence is leading to …
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Emerging Therapies Committee at UC Davis Hits the Accelerator Not the Brake | AMCP 2024
18 Apr 2024 21:40 GMT
… million gene therapy treatment for Duchenne muscular dystrophy, just 43 days after the …
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Gene Therapy: Non-Viral Vectors
18 Apr 2024 17:08 GMT
… delivered to mouse models of Duchenne muscular dystrophy (DMD) to correct the faulty …
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Biophytis Announces New Scientific Advisory Board for its Phase 2 OBA Clinical Study in Obesity
18 Apr 2024 11:14 GMT
… (sarcopenia, phase 3 ready and Duchenne muscular dystrophy), respiratory (Covid-19 phase 2 …
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Are Value-Based Contracts the Answer to Ultra-High-Priced Gene Therapies? | AMCP 2024
17 Apr 2024 21:25 GMT
… million; Elevidys (delandistrogene moxeparvovec) for Duchenne muscular dystrophy at $3.2 million; Hemgenix …