-
'You can start treatments right away'; Arizona family pushes to get all newborns screened for deadly muscular dystrophy
19 Apr 2024 12:48 GMT
… would expand the medical conditions that newborns … Duchenne muscular dystrophy to the screening process.
Anthony Castle, 24, has Duchenne muscular dystrophy … milestones late, but doctors assured her that … in clinical trials, he started getting treatment at age …
-
Parent Project Muscular Dystrophy Launches First State-Specific Duchenne Advocacy Day in Illinois
17 Apr 2024 07:35 GMT
… the fight to end Duchenne muscular dystrophy (Duchenne), is proud to announce … practices for providing medical guidance for Duchenne.
"The … healthcare providers, cutting edge treatments, and a community … funding and won eight FDA approvals.
Everything we …
-
Edgewise reports data from trial of muscular dystrophy drug
16 Apr 2024 13:00 GMT
US-based biotechnology company Edgewise … Duchenne muscular dystrophy.
The open-label, single-centre trial evaluated the drug … that the sevasemten treatment to reduce contraction- … disease progression.
Edgewise chief medical officer Joanne Donovan said …
-
Edgewise Therapeutics Announces Positive Two-Year Topline Results from the ARCH Open Label Trial of Sevasemten (EDG-5506) in Adults with Becker Muscular Dystrophy (Becker)
15 Apr 2024 20:10 GMT
… including Becker and Duchenne muscular dystrophy (Duchenne).
This press … Muscular Dystrophy
Presenter: Joanne Donovan, M.D., Ph.D., Chief Medical … clinical programs, and treatment guidelines to improve … trials; Edgewise’s ability to develop a proprietary drug …
-
Seven biotech companies climbing their way up in Colorado
16 Apr 2024 16:21 GMT
… trial of its valproate solution, CT-010, for the treatment … precision medicines.
Edgewise’s EDG-5506 treats muscular dystrophy. … damage in Duchenne and Becker Muscular Dystrophy, which are … January, the biotech earned Investigational New Drug (IND) status …
-
Hospital gives first dose of gene therapy for DMD in WV
19 Apr 2024 16:47 GMT
… gene therapy for Duchenne Muscular Dystrophy (DMD), providing potentially life-altering treatment for children … by the FDA in January.
According to a release, Duchenne Muscular Dystrophy is an … over time.
According to WVU Medicine, early studies with gene …
-
Inspired by idol Messi, S’porean soccer player, 23, strives to dribble & feint like him but in a wheelchair
19 Apr 2024 11:51 GMT
… sportsman Tan was diagnosed with Duchenne Muscular Dystrophy (DMD) when he was just … .
He was introduced by the Muscular Dystrophy Association (MDAS) to power soccer …
-
Emerging Therapies Committee at UC Davis Hits the Accelerator Not the Brake | AMCP 2024
18 Apr 2024 21:40 GMT
… nusinersen), the new, expensive drug for spinal muscular atrophy, “ … treatment for Duchenne muscular dystrophy, just 43 days after the FDA approved the drug … .
The criteria for drugs coming under the emerging … (cerliponase alfa), a treatment for a form of …
-
Biophytis Announces New Scientific Advisory Board for its Phase 2 OBA Clinical Study in Obesity
18 Apr 2024 11:14 GMT
… FDA in the coming weeks.
Prof. Dennis Villareal, Professor of Medicine … respect to optimal treatment strategies for older … biotechnology company specializing in the development of drug … phase 3 ready and Duchenne muscular dystrophy), respiratory (Covid-19 …
-
Venture 50: Early-stage research & development draw investors to clean tech & life sciences sector
18 Apr 2024 22:47 GMT
… its potential to treat Duchenne muscular dystrophy.
That confidence is … (TSXV: NGEN), another biotech company on the 2024 Venture … Food and Drug Administration to begin clinical trials for a … , from developing novel medical treatments to pioneering new clean …